Department of Laboratory Medicine and Pathology, Mayo Clinic, Rochester, MN 55905, USA.
Department of Quantitative Health Sciences, Mayo Clinic, Rochester, MN 55905, USA.
Hum Pathol. 2023 Sep;139:27-36. doi: 10.1016/j.humpath.2023.06.007. Epub 2023 Jun 28.
The gastrointestinal (GI) tract is a common site of amyloidosis, but the incidence, clinicopathologic features, and systemic implications of different types of GI amyloidosis are not well understood. GI amyloid specimens (N = 2511) typed using a proteomics-based method between 2008 and 2021 were identified. Clinical and morphologic features were reviewed in a subset of cases. Twelve amyloid types were identified, including AL (77.9%), ATTR (11.3%), AA (6.6%), AH (1.1%), AApoAIV (1.1%), AEFEMP1 (0.7%), ALys (0.4%), AApoAI (0.4%), ALECT2 (0.2%), Aβ2M (0.1%), AGel (0.1%), and AFib (<0.1%). Amino acid abnormalities indicative of known amyloidogenic mutations were detected in 24.4% ATTR cases. AL, ATTR, and AA types all commonly involved submucosal vessels. They also showed some characteristic patterns of involvement of more superficial anatomic compartments, although there was significant overlap. Common indications for biopsy were diarrhea, GI bleed, abdominal pain, or weight loss. Amyloidosis was usually an unexpected finding, but most AL and ATTR patients were ultimately found to have cardiac involvement (83.5% of AL; 100% of ATTR). Although most GI amyloid is of AL type, over 10% are ATTR, over 5% are AA, and twelve different types were identified in total. GI amyloid is often unexpected but usually signals systemic amyloidosis, thus there should be a low threshold to perform biopsy with Congo red stain in patients with unexplained GI symptoms. Clinical and histologic features are nonspecific, and typing should be performed via a robust method such as proteomics as treatment hinges on correctly identifying the amyloid type.
胃肠道(GI)是淀粉样变的常见部位,但不同类型的 GI 淀粉样变的发病率、临床病理特征和全身影响尚不清楚。在 2008 年至 2021 年间,使用基于蛋白质组学的方法对 2511 例 GI 淀粉样变标本进行了分型。在部分病例中回顾了临床和形态学特征。确定了 12 种淀粉样蛋白类型,包括 AL(77.9%)、ATTR(11.3%)、AA(6.6%)、AH(1.1%)、AApoAIV(1.1%)、AEFEMP1(0.7%)、ALys(0.4%)、AApoAI(0.4%)、ALECT2(0.2%)、Aβ2M(0.1%)、AGel(0.1%)和 AFib(<0.1%)。在 24.4%的 ATTR 病例中检测到提示已知淀粉样变性突变的氨基酸异常。AL、ATTR 和 AA 型均常见于黏膜下血管。它们还表现出一些更浅表解剖部位受累的特征性模式,尽管存在明显的重叠。活检的常见指征是腹泻、GI 出血、腹痛或体重减轻。淀粉样变通常是意外发现,但大多数 AL 和 ATTR 患者最终被发现有心脏受累(83.5%的 AL;100%的 ATTR)。尽管大多数 GI 淀粉样变是 AL 型,但超过 10%是 ATTR,超过 5%是 AA,总共确定了 12 种不同类型。GI 淀粉样变通常是意外的,但通常表明系统性淀粉样变,因此对于原因不明的 GI 症状患者,应低阈值进行刚果红染色活检。临床和组织学特征是非特异性的,应通过蛋白质组学等强大方法进行分型,因为治疗取决于正确识别淀粉样蛋白类型。