Shanghai Engineering Research Center of Molecular Therapeutics and New Drug Development, School of Chemistry and Molecular Engineering, East China Normal University, Shanghai, 200062, People's Republic of China.
Division of Anti-Tumor Pharmacology, State Key Laboratory of Drug Research, Shanghai Institute of Materia Medica, Chinese Academy of Sciences, Shanghai, 201203, People's Republic of China.
Mol Divers. 2024 Aug;28(4):2617-2636. doi: 10.1007/s11030-023-10701-y. Epub 2023 Jul 23.
Throughout the reported applications of EGFR inhibitors, it is usually employed with HDAC or other targets to design multi-target inhibitors for cancer treatment. In this paper, we designed a drug conjugate that targeted EGFR&HER2 and had inhibitory activity of NAMPT simultaneously. Compound 20c significantly inhibited the EGFR&HER2 and NAMPT enzyme activities, and had comparable or even higher anti-proliferative activity than lapatinib in various cancer cells with over-expressed EGFR and HER2. Importantly, 20c was expected to increase sensitivity to EGFR inhibitor-resistant cells. In Osimertinib-resistant cells (NCI-1975 cells with the L858R/T790M/C797S triple mutation and Ba/F3 cells with the Del19/T790M/C797S triple mutation), the anti-proliferative activity of compound 20c was increased by more than twofold compared with Osimertinib, so as to obtain better curative effect. This strategy is a promising method of embedding multiple pharmacophores into a single molecule, which lays a good foundation for the design and synthesis of small molecule drug conjugates with strong targeting ability and high cytotoxicity.
在已报道的 EGFR 抑制剂的应用中,通常与 HDAC 或其他靶点联合使用,以设计用于癌症治疗的多靶标抑制剂。在本文中,我们设计了一种靶向 EGFR&HER2 并具有 NAMPT 抑制活性的药物偶联物。化合物 20c 显著抑制 EGFR&HER2 和 NAMPT 酶活性,并且在各种过表达 EGFR 和 HER2 的癌细胞中具有与拉帕替尼相当甚至更高的抗增殖活性。重要的是,20c 有望增加对 EGFR 抑制剂耐药细胞的敏感性。在奥希替尼耐药细胞(具有 L858R/T790M/C797S 三重突变的 NCI-1975 细胞和具有 Del19/T790M/C797S 三重突变的 Ba/F3 细胞)中,与奥希替尼相比,化合物 20c 的抗增殖活性增加了两倍以上,从而获得更好的疗效。这种策略是将多个药效团嵌入单个分子中的一种很有前途的方法,为设计和合成具有强靶向性和高细胞毒性的小分子药物偶联物奠定了良好的基础。