Department of Chemistry and Molecular Biology, University of Gothenburg; S-405 30, Gothenburg, Sweden.
Department of Chemistry, University of Bergen, Allegaten 41, NO-5007, Bergen, Norway.
Nat Commun. 2023 Sep 5;14(1):5408. doi: 10.1038/s41467-023-41119-7.
Drugs targeting multiple stages of the Plasmodium vivax life cycle are needed to reduce the health and economic burdens caused by malaria worldwide. N-myristoyltransferase (NMT) is an essential eukaryotic enzyme and a validated drug target for combating malaria. However, previous PvNMT inhibitors have failed due to their low selectivity over human NMTs. Herein, we apply a structure-guided hybridization approach combining chemical moieties of previously reported NMT inhibitors to develop the next generation of PvNMT inhibitors. A high-resolution crystal structure of PvNMT bound to a representative selective hybrid compound reveals a unique binding site architecture that includes a selective conformation of a key tyrosine residue. The hybridized compounds significantly decrease P. falciparum blood-stage parasite load and consistently exhibit dose-dependent inhibition of P. vivax liver stage schizonts and hypnozoites. Our data demonstrate that hybridized NMT inhibitors can be multistage antimalarials, targeting dormant and developing forms of liver and blood stage.
需要针对间日疟原虫生命周期多个阶段的药物来减轻全球疟疾造成的健康和经济负担。N-豆蔻酰转移酶(NMT)是一种必需的真核酶,也是抗疟的有效药物靶点。然而,由于先前的 PvNMT 抑制剂对人 NMT 的选择性较低,因此它们都失败了。在此,我们应用结构指导的杂交方法将先前报道的 NMT 抑制剂的化学部分结合起来,开发新一代的 PvNMT 抑制剂。与代表性选择性杂合化合物结合的 PvNMT 的高分辨率晶体结构揭示了一个独特的结合位点结构,其中包括一个关键酪氨酸残基的选择性构象。杂交化合物可显著降低恶性疟原虫血期寄生虫载量,并一致表现出对间日疟原虫肝期裂殖体和休眠子的剂量依赖性抑制作用。我们的数据表明,杂交 NMT 抑制剂可以是多阶段抗疟药物,针对休眠和发育中的肝期和血期。