Department of Hematology, Kanagawa Cancer Center, Yokohama, Japan.
Hematology Division, Tokyo Metropolitan Cancer and Infectious Diseases Center, Komagome Hospital, Tokyo, Japan.
Hematology. 2024 Dec;29(1):2360843. doi: 10.1080/16078454.2024.2360843. Epub 2024 Jun 3.
The outcomes of relapsed Philadelphia chromosome-positive acute lymphoblastic leukemia (Ph+ALL) resistant to new drugs such as tyrosine kinase inhibitors, inotuzumab ozogamicin (InO) and blinatumomab are dismal. We treated two cases of Ph+ALL resistant to these drugs that achieved long-term survival after treatment with chimeric antigen receptor (CAR)-T cell therapy or a second allogeneic hematopoietic stem cell transplantation (HCT) with a sequential conditioning regimen. Case 1: A 15-year-old boy was diagnosed with Ph+ALL. Despite the second HCT after the treatment of ponatinib and blinatumomab, hematological relapse occurred. InO was ineffective and he was transferred to a CAR-T center. After the CAR-T cell therapy, negative measurable residual disease (MRD) was achieved and maintained for 38 months without maintenance therapy. Case 2: A 21-year-old man was diagnosed with Ph+ALL. Hematological relapse occurred after the first HCT. Despite of the treatment with InO, ponatinib, and blinatumomab, hematological remission was not achieved. The second HCT was performed using a sequential conditioning regimen with clofarabine. Negative MRD was subsequently achieved and maintained for 42 months without maintenance therapy. These strategies are suggestive and helpful to treat Ph+ALL resistant to multiple immunotherapies.
对于新药物(如酪氨酸激酶抑制剂、依鲁替尼奥佐米星(InO)和blinatumomab)耐药的复发费城染色体阳性急性淋巴细胞白血病(Ph+ALL)患者,其结局令人沮丧。我们治疗了两例对这些药物耐药的 Ph+ALL 患者,他们在接受嵌合抗原受体(CAR)-T 细胞治疗或序贯预处理的第二次异基因造血干细胞移植(HCT)后,实现了长期生存。
病例 1:一名 15 岁男孩被诊断为 Ph+ALL。尽管在 ponatinib 和blinatumomab 治疗后进行了第二次 HCT,但仍出现血液学复发。InO 无效,他被转至 CAR-T 中心。CAR-T 细胞治疗后,达到了阴性可测量残留病(MRD),并持续了 38 个月,没有维持治疗。
病例 2:一名 21 岁男性被诊断为 Ph+ALL。第一次 HCT 后出现血液学复发。尽管使用了 InO、ponatinib 和blinatumomab 治疗,但血液学缓解并未实现。采用 clofarabine 序贯预处理进行了第二次 HCT。随后达到了阴性 MRD,并持续了 42 个月,没有维持治疗。
这些策略为治疗对多种免疫疗法耐药的 Ph+ALL 提供了有价值的思路和帮助。