Safety and efficacy of aceneuramic acid in GNE myopathy: open-label extension study.
作者信息
Suzuki Naoki, Mori-Yoshimura Madoka, Katsuno Masahisa, Takahashi Masanori P, Yamashita Satoshi, Oya Yasushi, Hashizume Atsushi, Yamada Shinichiro, Nakamori Masayuki, Izumi Rumiko, Kato Masaaki, Warita Hitoshi, Tateyama Maki, Kuroda Hiroshi, Asada Ryuta, Yamaguchi Takuhiro, Nishino Ichizo, Aoki Masashi
机构信息
Department of Neurology, Tohoku University Graduate School of Medicine, Sendai, Japan.
Department of Neurology, National Center Hospital, National Center of Neurology and Psychiatry (NCNP), Tokyo, Japan.
出版信息
J Neurol Neurosurg Psychiatry. 2024 Oct 16;95(11):1093-1094. doi: 10.1136/jnnp-2024-333853.
Abstract
摘要
Zotero 插件