In vivo genome editing for inherited retinal disease: Opportunities and challenges.
作者信息
Collin Rob W J, Leroy Bart P
机构信息
Department of Human Genetics, Radboud Institute for Medical Innovation, Radboud University Medical Center, Nijmegen, the Netherlands.
Center for Medical Genetics Ghent (CMGG), Ghent University Hospital, Ghent, Belgium; Department of Ophthalmology, Ghent University Hospital, Ghent, Belgium; Department of Head & Skin, Ghent University, Ghent, Belgium.
出版信息
Mol Ther. 2024 Aug 7;32(8):2433-2434. doi: 10.1016/j.ymthe.2024.07.001. Epub 2024 Jul 30.
Abstract
摘要
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