Weighing the Risks of Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy.
作者信息
Dunbar Cynthia E
机构信息
From the Translational Stem Cell Biology Branch, National Heart, Lung, and Blood Institute, National Institutes of Health, Bethesda, Maryland.
出版信息
N Engl J Med. 2024 Oct 10;391(14):1358-1359. doi: 10.1056/NEJMe2409399.
PMID:39383463
Abstract
摘要
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