Cai Shiru, Xu Shenglong, Zhao Yan, Zhang Luo
Department of Otolaryngology Head and Neck Surgery, Beijing TongRen Hospital, Capital Medical University, Beijing, People's Republic of China.
Beijing Institute of Otorhinolaryngology, Beijing Key Laboratory of Nasal Diseases and Beijing Laboratory of Allergic Diseases, Beijing, People's Republic of China.
Allergy. 2025 May;80(5):1256-1270. doi: 10.1111/all.16499. Epub 2025 Feb 22.
Dupilumab, omalizumab, mepolizumab, and benralizumab have demonstrated good efficacy and safety in the treatment of severe uncontrolled chronic rhinosinusitis with nasal polyps (CRSwNP) in phase 3 randomised controlled trials (RCTs). With recent regulatory approvals, there has been a surge in real-world studies (RWSs). This systematic review and meta-analysis aimed to summarise the efficacy and safety of these four biologics in real-world settings. Primary outcomes were nasal polyp score and sino-nasal outcome test-22 score. Secondary outcomes included smell identification test score, loss of smell score, nasal congestion score, overall nasal symptom score, treatment response, and adverse events (AEs) prompting discontinuation. Efficacy outcomes at 4, 6, 12, and over 12 months were summarised, and meta-analyses of mean changes from baseline were conducted. Sixty-four RWSs involving 3921 patients were included. Significant improvements in clinical outcomes were observed at most follow-up time points, with dupilumab showing particularly notable effects. The efficacy observed in these RWSs was superior to that demonstrated in phase 3 RCTs. All biologics exhibited low discontinuation rates due to AEs. Overall, biologic treatments for CRSwNP in real-world settings demonstrate strong efficacy and good safety. However, the limitations in current RWSs highlight the need for long-term, high-quality multicentre prospective studies and comprehensive healthcare database analyses.
度普利尤单抗、奥马珠单抗、美泊利单抗和贝那利珠单抗在3期随机对照试验(RCT)中已证明对治疗伴有鼻息肉的严重难治性慢性鼻-鼻窦炎(CRSwNP)具有良好的疗效和安全性。随着近期获得监管批准,真实世界研究(RWS)激增。本系统评价和荟萃分析旨在总结这四种生物制剂在真实世界中的疗效和安全性。主要结局指标为鼻息肉评分和鼻窦结局测试-22评分。次要结局指标包括嗅觉识别测试评分、嗅觉丧失评分、鼻充血评分、总体鼻部症状评分、治疗反应以及导致停药的不良事件(AE)。总结了4、6、12个月及12个月以上的疗效结局,并对与基线相比的平均变化进行了荟萃分析。纳入了64项涉及3921例患者的RWS。在大多数随访时间点均观察到临床结局有显著改善,度普利尤单抗的效果尤为显著。这些RWS中观察到的疗效优于3期RCT中显示的疗效。所有生物制剂因AE导致的停药率均较低。总体而言,真实世界中CRSwNP的生物制剂治疗显示出强大的疗效和良好的安全性。然而,当前RWS的局限性凸显了开展长期、高质量多中心前瞻性研究以及全面医疗保健数据库分析的必要性。