Broughton B C, Thompson A F, Harcourt S A, Vermeulen W, Hoeijmakers J H, Botta E, Stefanini M, King M D, Weber C A, Cole J
MRC Cell Mutation Unit, University of Sussex, Falmer, Brighton, United Kingdom.
Am J Hum Genet. 1995 Jan;56(1):167-74.
Xeroderma pigmentosum (XP) and Cockayne syndrome (CS) are quite distinct genetic disorders that are associated with defects in excision repair of UV-induced DNA damage. A few patients have been described previously with the clinical features of both disorders. In this paper we describe an individual in this category who has unusual cellular responses to UV light. We show that his cultured fibroblasts and lymphocytes are extremely sensitive to irradiation with UV-C, despite a level of nucleotide excision repair that is 30%-40% that of normal cells. The deficiency is assigned to the XP-D complementation group, and we have identified two causative mutations in the XPD gene: a gly-->arg change at amino acid 675 in the allele inherited from the patient's mother and a -1 frameshift at amino acid 669 in the allele inherited from his father. These mutations are in the C-terminal 20% of the 760-amino-acid XPD protein, in a region where we have recently identified several mutations in patients with trichothiodystrophy.
着色性干皮病(XP)和科凯恩综合征(CS)是截然不同的遗传性疾病,与紫外线诱导的DNA损伤切除修复缺陷相关。此前已描述过一些具有这两种疾病临床特征的患者。在本文中,我们描述了这一类型中的一名个体,其对紫外线具有异常的细胞反应。我们发现,尽管其核苷酸切除修复水平仅为正常细胞的30%-40%,但其培养的成纤维细胞和淋巴细胞对紫外线C照射极为敏感。这种缺陷被归为XP-D互补组,我们在XPD基因中鉴定出两个致病突变:从患者母亲遗传的等位基因中第675位氨基酸处的甘氨酸→精氨酸变化,以及从其父亲遗传的等位基因中第669位氨基酸处的-1移码突变。这些突变位于760个氨基酸的XPD蛋白的C末端20%区域,我们最近在毛发硫营养不良患者中也在该区域鉴定出了几个突变。