磷脂酰肌醇蛋白聚糖基因GPC3的突变会导致辛普森-戈拉比-贝梅尔过度生长综合征。
Mutations in GPC3, a glypican gene, cause the Simpson-Golabi-Behmel overgrowth syndrome.
作者信息
Pilia G, Hughes-Benzie R M, MacKenzie A, Baybayan P, Chen E Y, Huber R, Neri G, Cao A, Forabosco A, Schlessinger D
机构信息
Center for Genetics in Medicine, Washington University School of Medicine, St. Louis, Missouri 63110, USA.
出版信息
Nat Genet. 1996 Mar;12(3):241-7. doi: 10.1038/ng0396-241.
Simpson-Golabi-Behmel syndrome (SGBS) is an X-linked condition characterized by pre- and postnatal overgrowth with visceral and skeletal anomalies. To identify the causative gene, breakpoints in two female patients with X;autosome translocations were identified. The breakpoints occur near the 5' and 3' ends of a gene, GPC3, that spans more than 500 kilobases in Xq26; in three families, different microdeletions encompassing exons cosegregate with SGBS. GPC3 encodes a putative extracellular proteoglycan, glypican 3, that is inferred to play an important role in growth control in embryonic mesodermal tissues in which it is selectively expressed. Initial western- and ligand-blotting experiments suggest that glypican 3 forms a complex with insulin-like growth factor 2 (IGF2), and might thereby modulate IGF2 action.
辛普森-戈拉比-贝梅尔综合征(SGBS)是一种X连锁疾病,其特征为出生前后过度生长并伴有内脏和骨骼异常。为了鉴定致病基因,确定了两名患有X;常染色体易位的女性患者的断点。这些断点出现在一个基因GPC3的5'和3'端附近,该基因在Xq26中跨度超过500千碱基;在三个家族中,包含外显子的不同微缺失与SGBS共分离。GPC3编码一种假定的细胞外蛋白聚糖——磷脂酰肌醇蛋白聚糖3,据推测它在其选择性表达的胚胎中胚层组织的生长控制中起重要作用。最初的蛋白质免疫印迹和配体印迹实验表明,磷脂酰肌醇蛋白聚糖3与胰岛素样生长因子2(IGF2)形成复合物,从而可能调节IGF2的作用。