Cautious advance. Gene therapy is more complex than anticipated.
作者信息
Fischer A
机构信息
Unite d'Immunologie et d'Hematologie Pediatriques, INSERM Unit 429 of the H pital Necker in Paris.
出版信息
EMBO Rep. 2000 Oct;1(4):294-6. doi: 10.1093/embo-reports/kvd085.
Abstract
摘要
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本文引用的文献
1
Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin.在表达慢病毒编码的人β-珠蛋白的β地中海贫血小鼠中进行治疗性血红蛋白合成。
Nature. 2000 Jul 6;406(6791):82-6. doi: 10.1038/35017565.
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Gene therapy using hematopoietic stem cells: Sisyphus approaches the crest.利用造血干细胞的基因治疗：西西弗斯接近顶峰。
Hum Gene Ther. 2000 Jun 10;11(9):1259-67. doi: 10.1089/10430340050032366.
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Gene therapy's web of corporate connections.基因治疗的企业关联网络。
Science. 2000 May 12;288(5468):954-5. doi: 10.1126/science.288.5468.954.
4
Efficient retrovirus-mediated transfer of the multidrug resistance 1 gene into autologous human long-term repopulating hematopoietic stem cells.高效逆转录病毒介导的多药耐药1基因转移至自体人类长期造血干细胞中。
Nat Med. 2000 Jun;6(6):652-8. doi: 10.1038/76225.
5
Physician-scientists: mind the gap.医学科学家：注意差距。
Nat Med. 2000 Jun;6(6):605. doi: 10.1038/76133.
6
Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease.人类重症联合免疫缺陷（SCID）-X1病的基因治疗。
Science. 2000 Apr 28;288(5466):669-72. doi: 10.1126/science.288.5466.669.
7
Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors.通过HIV载体转导介导NOD/SCID小鼠长期植入的人CD34+细胞。
Science. 1999 Jan 29;283(5402):682-6. doi: 10.1126/science.283.5402.682.
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