Powell Steven M
Division of Gastroenterology, University of Virginia Health System, Charlottesville 22908, USA.
Mol Biotechnol. 2002 Feb;20(2):197-207. doi: 10.1385/MB:20:2:197.
The spectrum of disease causing mutations is immense. It just so happens that the overwhelming majority of genetic alterations in the APC gene with leads to adenomatous polyposis coli generate truncated gene products. This observation lead to the development of the in vitro synthesis protein assay (protein truncation test) which is a sensitive method to detect these truncated gene products from patient samples. This article describes the assay to detect truncated proteins for the APC gene, which can also be applied to other disease causing genetic alterations which commonly lead to truncations such in HNPCC, von Hippel-Lindau, osteogenesis imperfecta, retinoblastoma, BCRAI, beta-thalassemia, hemophilia B, Duchenene and Becker muscular dystrophy.
导致疾病的突变谱极为广泛。恰好,导致腺瘤性息肉病的APC基因中的绝大多数基因改变会产生截短的基因产物。这一观察结果促使了体外合成蛋白检测法(蛋白截短检测)的发展,该方法是一种从患者样本中检测这些截短基因产物的灵敏方法。本文描述了检测APC基因截短蛋白的检测方法,该方法也可应用于其他通常导致截短的致病基因改变,如遗传性非息肉病性结直肠癌、冯·希佩尔-林道病、成骨不全症、视网膜母细胞瘤、乳腺癌1号基因、β地中海贫血、血友病B、杜氏和贝克肌营养不良症。