Wasserman Zelda R, Duan James J-W, Voss Matthew E, Xue Chu Biao, Cherney Robert J, Nelson David J, Hardman Karl D, Decicco Carl P
Structural Biology and Molecular Design Group, Bristol-Myers Squibb Company, Experimental Station, Wilmington, DE 19880, USA.
Chem Biol. 2003 Mar;10(3):215-23. doi: 10.1016/s1074-5521(03)00044-9.
Inhibition of tumor necrosis factor-alpha converting enzyme (TACE) is a widespread objective in the search for disease modifying agents to combat rheumatoid arthritis and other autoimmune diseases. Until recently, most of the inhibitors in the literature have shown concomitant activity against the related matrix metalloproteinases (MMPs), producing undesired side effects. Here we describe the successful search for a TACE selectivity mechanism. We built a homology model based on the crystal structure of the related snake venom protein atrolysin. Comparison of the model with crystal structures of MMPs suggested a uniquely shaped S1' pocket that might be exploited for selectivity. A novel gamma-lactam scaffold was used to explore the activity profile of P1' sidechains, resulting in highly selective compounds consistent with this hypothesis. Transferability of the hypothesis was then demonstrated with five other distinct scaffolds.
抑制肿瘤坏死因子-α转化酶(TACE)是寻找用于对抗类风湿性关节炎和其他自身免疫性疾病的疾病修饰剂的一个广泛目标。直到最近,文献中的大多数抑制剂都显示出对相关基质金属蛋白酶(MMP)的伴随活性,产生了不良副作用。在此,我们描述了成功寻找TACE选择性机制的过程。我们基于相关蛇毒蛋白阿特罗溶素的晶体结构构建了一个同源模型。该模型与MMP晶体结构的比较表明,存在一个形状独特的S1'口袋,可用于实现选择性。一种新型γ-内酰胺支架被用于探索P1'侧链的活性概况,得到了与该假设一致的高选择性化合物。然后用其他五种不同的支架证明了该假设的可转移性。