McCarthy Mark I
Oxford Centre for Diabetes, Endocrinology and Metabolism, Churchill Hospital Site, Headington, Oxford OX3 7LJ and Wellcome Trust Centre for Human Genetics, Oxford OX3 7BN, UK.
Hum Mol Genet. 2004 Apr 1;13 Spec No 1:R33-41. doi: 10.1093/hmg/ddh057. Epub 2004 Jan 13.
The rapid increase in the prevalence of type 2 diabetes (T2D) represents a major challenge for health care delivery worldwide. Identification of genes influencing individual susceptibility to disease offers a route to better understanding of the molecular mechanisms underlying pathogenesis, a necessary prerequisite for the rational development of improved preventative and therapeutic methods. The past decade has seen substantial success in identifying genes responsible for monogenic forms of diabetes (notably, maturity-onset diabetes of the young), and, in patients presenting with early-onset diabetes, a precise molecular diagnosis is an increasingly important element of optimal clinical care. Progress in gene identification for more common, multifactorial forms of type 2 diabetes has been slower, but there is now compelling evidence that common variants in the PPARG, KCNJ11 and CAPN10 genes influence T2D-susceptibility, and positional cloning efforts within replicated regions of linkage promise to deliver additional components of inherited susceptibility. The challenge in the years to come will be to understand how T2D risk is influenced by the interaction of these variants with each other and with pertinent environmental factors encountered during gestation, childhood and adulthood; and to establish how best to apply this understanding to provide individuals with clinically-useful diagnostic, prognostic and therapeutic information.
2型糖尿病(T2D)患病率的迅速上升对全球医疗保健服务构成了重大挑战。识别影响个体疾病易感性的基因,为更好地理解发病机制的分子机制提供了一条途径,而这是合理开发改进的预防和治疗方法的必要前提。在过去十年中,在识别导致单基因形式糖尿病(特别是青少年成年发病型糖尿病)的基因方面取得了重大成功,并且对于早发型糖尿病患者而言,精确的分子诊断已日益成为最佳临床护理的重要组成部分。对于更常见的多因素形式的2型糖尿病,基因识别方面的进展较为缓慢,但现在有令人信服的证据表明,PPARG、KCNJ11和CAPN10基因中的常见变异会影响T2D易感性,并且在连锁复制区域内进行的定位克隆工作有望揭示遗传易感性的其他组成部分。未来几年的挑战将是了解这些变异彼此之间以及与妊娠、儿童期和成年期所遇到的相关环境因素的相互作用如何影响T2D风险;并确定如何最好地应用这一认识,为个体提供具有临床实用性的诊断、预后和治疗信息。