Campos Samuel K, Parrott M Brandon, Barry Michael A
Department of Biochemistry and Cell Biology, Rice University, Houston, TX 77005, USA.
Mol Ther. 2004 Jun;9(6):942-54. doi: 10.1016/j.ymthe.2004.03.006.
While genetic modification of adenoviral vectors can produce vectors with modified tropism, incorporation of targeting peptides/proteins into the structural context of the virion can also result in destruction of ligand targeting or virion integrity. To combat this problem, we have developed a versatile targeting system using metabolically biotinylated adenoviral vectors bearing biotinylated fiber proteins. These vectors have been demonstrated to be useful as a platform for avidin-based ligand screening and vector targeting by conjugating biotinylated ligands to the virus using high-affinity tetrameric avidin (K(d) = 10(-15) M). The biotinylated vector could also be purified by biotin-reversible binding on monomeric avidin (K(d) = 10(-7) M). In this report, a second metabolically biotinylated adenovirus vector, Ad-IX-BAP, has been engineered by fusing a biotin acceptor peptide (BAP) to the C-terminus of the adenovirus pIX protein. This biotinylated vector displays twice as many biotins and was markedly superior for single-step affinity purification on monomeric avidin resin. However, unlike the fiber-biotinylated vector, Ad-IX-BAP failed to retarget to cells with biotinylated antibodies including anti-CD71 against the transferrin receptor. In contrast, Ad-IX-BAP was retargeted if transferrin, the cognate ligand for CD71, was used as a ligand rather than the anti-CD71. This work demonstrates the utility of metabolic biotinylation as a molecular screening tool to assess the utility of different viral capsid proteins for ligand display and the biology and compatibility of different ligands and receptors for vector targeting applications. These results also demonstrate the utility of the pIX-biotinylated vector as a platform for gentle single-step affinity purification of adenoviral vectors.
虽然腺病毒载体的基因改造可产生具有改变嗜性的载体,但将靶向肽/蛋白质整合到病毒粒子的结构中也可能导致配体靶向破坏或病毒粒子完整性受损。为了解决这个问题,我们开发了一种通用的靶向系统,该系统使用带有生物素化纤维蛋白的代谢性生物素化腺病毒载体。这些载体已被证明可作为基于抗生物素蛋白的配体筛选和载体靶向的平台,通过使用高亲和力的四聚体抗生物素蛋白(K(d)=10(-15) M)将生物素化配体与病毒偶联。生物素化载体还可通过与单体抗生物素蛋白(K(d)=10(-7) M)的生物素可逆结合进行纯化。在本报告中,通过将生物素接受肽(BAP)融合到腺病毒pIX蛋白的C末端,构建了第二种代谢性生物素化腺病毒载体Ad-IX-BAP。这种生物素化载体显示出两倍数量的生物素,并且在单体抗生物素蛋白树脂上进行单步亲和纯化时明显更优。然而,与纤维生物素化载体不同,Ad-IX-BAP未能用包括抗转铁蛋白受体的抗CD71在内的生物素化抗体重新靶向细胞。相反,如果使用CD71的同源配体转铁蛋白作为配体而不是抗CD71,则Ad-IX-BAP会被重新靶向。这项工作证明了代谢性生物素化作为一种分子筛选工具的实用性,可用于评估不同病毒衣壳蛋白用于配体展示的效用以及不同配体和受体在载体靶向应用中的生物学特性和兼容性。这些结果还证明了pIX生物素化载体作为腺病毒载体温和单步亲和纯化平台的实用性。