Pareyson D
Division of Biochemistry and Genetics, C. Besta National Neurological Institute, Via Celoria 11, I-20133 Milan, Italy.
Neurol Sci. 2004 Jun;25(2):72-82. doi: 10.1007/s10072-004-0233-4.
The diagnosis of Charcot-Marie-Tooth disease (CMT) and related neuropathies (e. g. Déjèrine-Sottas disease; hereditary neuropathy with liability to pressure palsies) appears to be easy. However, the incredible advances in molecular genetics have greatly complicated the classification of these disorders, and the proper diagnosis of the CMT subtype may be important for correct genetic counselling and prognosis. Moreover, these diseases may be confused with potentially treatable acquired and inherited neuropathies, such as dysimmune neuropathies, familial amyloid polyneuropathy, and Refsum's disease. A number of clinical, laboratory, electrophysiological, morphological and neuroradiological features that may help in the diagnostic process are reviewed in the present paper. DNA investigations are fundamental but need to be properly addressed. Currently, great interest is focused on the role of the immune system in hereditary neuropathies, and surprising findings are coming from research on animal models.
夏科-马里-图斯病(CMT)及相关神经病变(如德热里纳-索塔斯病;遗传性压迫易感性神经病)的诊断看似容易。然而,分子遗传学的惊人进展极大地使这些疾病的分类变得复杂,正确诊断CMT亚型对于正确的遗传咨询和预后可能很重要。此外,这些疾病可能会与潜在可治疗的获得性和遗传性神经病变相混淆,如免疫性神经病变、家族性淀粉样多神经病和雷夫叙姆病。本文综述了一些可能有助于诊断过程的临床、实验室、电生理、形态学和神经放射学特征。DNA研究至关重要,但需要妥善处理。目前,人们高度关注免疫系统在遗传性神经病变中的作用,并且动物模型研究也有惊人发现。