Chrobák Ladislav, Hůlek Petr, Nozicka Jan
Univerzita Karlova v Praze, Lékarská fakulta Hradci Králové: II. interní klinika-Oddelení klinické hematologie.
Acta Medica (Hradec Kralove) Suppl. 2004;47(1):29-33.
The diagnosis of congenital dyserythropioetic anemia-type II (CDA-II) was established in 1974 in three siblings aged 20, 18 and 5 years, respectively. Liver biopsy performed in two elder siblings on admission revealed liver siderosis. Anemia showing haemolytic component with destruction of erythrocytes in the spleen was corrected after splenectomy. Increased number of erythrocytes showing "the double membrane phenomenon" was found in the peripheral blood after splenectomy. All three siblings developed cholecystolithiasis with choledocholithiasis and obstructive jaundice in two of them. Two patients at the age of 49 and 34 years (the third died in an accident at the age of 40 years) developed 29 years after the diagnosis of CDA-II had been established signs of iron overload with transferin saturation 99%, serum ferritin 1450.4 microg/l and 1131.7 microg/l respectively, and hepatic iron concentration (dry weight) 14,843 microg/g and 15,415 microg/g (norm 70-1400 microg/g) respectively. No mutations of HFE gene (C282Y and H63D) were found. Liver biopsy showed heavy accumulation of hemosiderin in hepatocytes and reticuloendothelial cells. The structure of the liver tissue was not changed, only mild fibrosis in portal area was present in the older patient. Because of iron overload therapy with phlebotomy once monthly (400 ml) has been started in both patients. In peripheral blood films excess of Pappenheimer bodies was found.
1974年,分别在一名20岁、一名18岁和一名5岁的三兄弟姐妹中确诊为II型先天性红细胞生成异常性贫血(CDA-II)。入院时对两名年长的兄弟姐妹进行肝脏活检,发现肝脏有含铁血黄素沉着症。贫血表现为具有脾脏红细胞破坏的溶血成分,脾切除术后得以纠正。脾切除术后在外周血中发现显示“双膜现象”的红细胞数量增加。所有三兄弟姐妹均患胆囊结石和胆总管结石,其中两人出现梗阻性黄疸。两名分别为49岁和34岁的患者(第三名患者在40岁时死于意外事故)在CDA-II确诊29年后出现铁过载迹象,转铁蛋白饱和度分别为99%,血清铁蛋白分别为1450.4μg/l和1131.7μg/l,肝铁浓度(干重)分别为14843μg/g和15415μg/g(正常范围70 - 1400μg/g)。未发现HFE基因(C282Y和H63D)突变。肝脏活检显示肝细胞和网状内皮细胞中有大量含铁血黄素沉积。肝组织结构未改变,仅年长患者的门静脉区域存在轻度纤维化。由于铁过载,已开始对两名患者每月进行一次静脉放血治疗(400ml)。在外周血涂片上发现有过多的环形铁粒幼红细胞。