Ma Jin-Biao, Yuan Yu-Ren, Meister Gunter, Pei Yi, Tuschl Thomas, Patel Dinshaw J
Structural Biology Program, Memorial Sloan-Kettering Cancer Center, New York, New York 10021, USA.
Nature. 2005 Mar 31;434(7033):666-70. doi: 10.1038/nature03514.
RNA interference (RNAi) is a conserved sequence-specific gene regulatory mechanism mediated by the RNA-induced silencing complex (RISC), which is composed of a single-stranded guide RNA and an Argonaute protein. The PIWI domain, a highly conserved motif within Argonaute, has been shown to adopt an RNase H fold critical for the endonuclease cleavage activity of RISC. Here we report the crystal structure of Archaeoglobus fulgidus Piwi protein bound to double-stranded RNA, thereby identifying the binding pocket for guide-strand 5'-end recognition and providing insight into guide-strand-mediated messenger RNA target recognition. The phosphorylated 5' end of the guide RNA is anchored within a highly conserved basic pocket, supplemented by the carboxy-terminal carboxylate and a bound divalent cation. The first nucleotide from the 5' end of the guide RNA is unpaired and stacks over a conserved tyrosine residue, whereas successive nucleotides form a four-base-pair RNA duplex. Mutation of the corresponding amino acids that contact the 5' phosphate in human Ago2 resulted in attenuated mRNA cleavage activity. Our structure of the Piwi-RNA complex, and that determined elsewhere, provide direct support for the 5' region of the guide RNA serving as a nucleation site for pairing with target mRNA and for a fixed distance separating the RISC-mediated mRNA cleavage site from the anchored 5' end of the guide RNA.
RNA干扰(RNAi)是一种由RNA诱导沉默复合体(RISC)介导的保守的序列特异性基因调控机制,RISC由单链引导RNA和一个AGO蛋白组成。PIWI结构域是AGO蛋白中一个高度保守的基序,已被证明具有对RISC内切酶切割活性至关重要的核糖核酸酶H折叠结构。在此,我们报道了嗜热栖热菌Piwi蛋白与双链RNA结合的晶体结构,从而确定了引导链5'端识别的结合口袋,并深入了解了引导链介导的信使RNA靶标识别。引导RNA的磷酸化5'端锚定在一个高度保守的碱性口袋中,该口袋由羧基末端的羧酸盐和结合的二价阳离子补充。引导RNA 5'端的第一个核苷酸未配对,并堆叠在一个保守的酪氨酸残基上,而后续核苷酸形成一个四碱基对的RNA双链体。在人类AGO2中,与5'磷酸基团接触的相应氨基酸发生突变,导致mRNA切割活性减弱。我们的Piwi-RNA复合体结构以及在其他地方确定的结构,为引导RNA的5'区域作为与靶标mRNA配对的成核位点以及RISC介导的mRNA切割位点与引导RNA锚定的5'端之间存在固定距离提供了直接支持。