Classen C F, Teigler-Schlegel A, Röttgers S, Reinhardt D, Döhner K, Debatin K M
University Children's Hospital Ulm, Prittwitzstr. 43, 89070, Ulm, Germany.
Ann Hematol. 2005 Nov;84(12):774-80. doi: 10.1007/s00277-005-1089-2. Epub 2005 Nov 12.
We describe a case of acute myeloid leukemia (AML) bearing the translocation t(11;17)(q23;q21). The morphological phenotype represented a monoblastic leukemia, AML French-American-British (FAB) M5a. Further analysis of the translocation revealed an involvement of the mixed-lineage leukemia (MLL) gene and a region closely proximal to the retinoic acid (RA) receptor alpha (RARA) gene. AMLs involving both a rearranged MLL and the 17q21 region, in which the RARA gene is located, have only been described in some individual cases. The functional role of this translocation is still unknown. Rearrangements of the MLL (11q23) gene in AML are usually related to the morphological phenotype FAB M5. In general, they are associated with an adverse prognosis. In acute promyelocytic leukemia, the translocation (15;17)(q22;q11-21) involving the RARA leads to a maturation arrest that can be overcome by RA, often inducing remission. In other forms of AML, however, the effects of RA are limited and diverse. To study whether RA might have a therapeutical potential in our case, we performed an in vitro analysis of RA effects on AML cells. We found that RA leads to enhanced cell death and up-regulation of CD38 and CD117. However, no hints of RA-induced in vitro differentiation were visible. Our data indicate that in AML cells bearing the t(11;17)(q23;q21), a differentiation arrest that is overcome by RA is not present. On the contrary, RA induces alterations in cellular regulation that are similar to the RA-induced changes observed in early hematogenic progenitors; thus, a possible therapeutical benefit of RA in such cases remains open.
我们描述了一例携带t(11;17)(q23;q21)易位的急性髓系白血病(AML)。形态学表型为单核细胞白血病,即法国-美国-英国(FAB)分型的M5a型。对该易位的进一步分析显示,混合谱系白血病(MLL)基因以及紧邻维甲酸(RA)受体α(RARA)基因的一个区域受累。同时涉及重排的MLL基因和RARA基因所在的17q21区域的AML,仅在一些个别病例中有过描述。这种易位的功能作用仍不清楚。AML中MLL(11q23)基因的重排通常与FAB M5形态学表型相关。一般来说,它们与不良预后相关。在急性早幼粒细胞白血病中,涉及RARA的t(15;17)(q22;q11-21)易位导致成熟停滞,而RA可以克服这种停滞,常常诱导缓解。然而,在其他形式的AML中,RA的作用有限且多样。为了研究RA在我们这个病例中是否具有治疗潜力,我们对RA对AML细胞的作用进行了体外分析。我们发现RA导致细胞死亡增加以及CD38和CD117上调。然而,未观察到RA诱导的体外分化迹象。我们的数据表明,在携带t(11;17)(q23;q21)的AML细胞中,不存在可被RA克服的分化停滞。相反,RA诱导细胞调节发生改变,这与在早期造血祖细胞中观察到的RA诱导变化相似;因此,RA在这类病例中可能的治疗益处仍不明确。