Jørgensen Karsten J, Johansen Helle Krogh, Gøtzsche Peter C
The Nordic Cochrane Centre, Rigshospitalet, Copenhagen, Denmark.
Trials. 2006 Jan 19;7:3. doi: 10.1186/1745-6215-7-3.
We have previously described how a series of trials sponsored by Pfizer of its antifungal drug, fluconazole, in cancer patients with neutropenia handicapped the control drug, amphotericin B, by flaws in design and analysis. We describe similar problems in two pivotal trials of Pfizer's new antifungal agent, voriconazole, published in a prestigious journal. In a non-inferiority trial, voriconazole was significantly inferior to liposomal amphothericin B, but the authors concluded that voriconazole was a suitable alternative. The second trial used amphothericin B deoxycholate as comparator, but handicapped the drug by not requiring pre-medication to reduce infusion-related toxicity or substitution with electrolytes and fluid to reduce nephrotoxicity, although the planned duration of treatment was 84 days. Voriconazole was given for 77 days on average, but the comparator for only 10 days, which precludes a meaningful comparison. In a random sample of 50 references to these trials, we found that the unwarranted conclusions were mostly uncritically propagated. It was particularly surprising that relevant criticism raised by the FDA related to the first trial was only quoted once, and that none of the articles noted the obvious flaws in the design of the second trial. We suggest that editors ensure that the abstract reflects fairly on the remainder of the paper, and that journals do not impose any time limit for accepting letters that point out serious weaknesses in a study that have not been noted before.
我们之前曾描述过辉瑞公司针对其抗真菌药物氟康唑在中性粒细胞减少的癌症患者中开展的一系列试验,这些试验在设计和分析上存在缺陷,使对照药物两性霉素B处于不利地位。我们在发表于一本著名期刊上的辉瑞新型抗真菌药物伏立康唑的两项关键试验中也发现了类似问题。在一项非劣效性试验中,伏立康唑明显不如脂质体两性霉素B,但作者得出结论称伏立康唑是一种合适的替代药物。第二项试验使用脱氧胆酸盐两性霉素B作为对照,但由于未要求进行预处理以降低输液相关毒性,也未进行电解质和液体替代以降低肾毒性,尽管计划治疗时长为84天,这使得该药物处于不利地位。伏立康唑平均给药77天,而对照药物仅给药10天,这使得无法进行有意义的比较。在对这些试验的50篇参考文献的随机抽样中,我们发现这些不合理的结论大多被不加批判地传播。特别令人惊讶的是,美国食品药品监督管理局(FDA)针对第一项试验提出的相关批评仅被引用过一次,而且没有一篇文章指出第二项试验设计中明显的缺陷。我们建议编辑确保摘要能公正地反映论文的其余部分,并且期刊不要对接受指出此前未被注意到的研究严重缺陷的信件设置任何时间限制。