启动对被忽视疾病的研究。

Cell. 2006 Nov 3;127(3):443-5. doi: 10.1016/j.cell.2006.10.022.

Unwilling to wait and hope for a cure, patients suffering from rare or little-studied diseases and their families are galvanizing research efforts and driving innovative approaches to develop new treatments.

患有罕见病或研究较少疾病的患者及其家属不愿坐等治愈方法出现，他们正在推动研究工作，并采用创新方法来开发新的治疗手段。