Courtens Winnie, Schramme Inge, Laridon Annick
Center of Human Genetics UCL, Cliniques Universitaires St-Luc Brussels, Brussels, Belgium.
Am J Med Genet A. 2008 Mar 15;146A(6):758-63. doi: 10.1002/ajmg.a.31910.
We report on two unrelated families where the probands presented with learning difficulties and a microduplication 22q11.2. In the first family the proband was a 7-year-old boy who was referred because of psychomotor retardation, behavioral problems, large weight and height, and mild dysmorphism. His father and one brother also had mental retardation and behavioral anomalies, and presented the same microduplication. In the second family only the proband had mild learning difficulties, but the same microduplication 22q11.2 was discovered in her sister, her asymptomatic mother and grandfather. No distinctly recognizable phenotype has been observed in the individuals from our two families diagnosed with microduplication 22q11.2. The marked clinical variability both inter- and intrafamilial, including the presence of a complete normal phenotype and the presence of high intellectual possibilities in two individuals with this microduplication 22q11.2 is remarkable. So far, 63 patients, corresponding to 35 families, with microduplication 22q11.2 have been described. The fact that microduplication 22q11.2 can be seen in individuals with a normal/near normal phenotype has been previously reported as well. We postulate that the clinical findings described so far could be due to ascertainment bias, since the most common reason for performing FISH 22 analyses is to exclude microdeletion. Future reports are needed to answer the question whether microduplication could be a non-pathogenic polymorphism or whether it is a real syndrome with a very large clinical variability and reduced penetrance.
我们报告了两个无亲缘关系的家庭,其中先证者表现出学习困难以及22q11.2微重复。在第一个家庭中,先证者是一名7岁男孩,因精神运动发育迟缓、行为问题、体重和身高超标以及轻度畸形而被转诊。他的父亲和一个兄弟也有智力发育迟缓及行为异常,并存在相同的微重复。在第二个家庭中,只有先证者有轻度学习困难,但在她的姐姐、无症状的母亲和外祖父中发现了相同的22q11.2微重复。在我们这两个被诊断为22q11.2微重复的家庭中的个体,未观察到明显可识别的表型。家族间和家族内显著的临床变异性,包括存在完全正常的表型以及两名患有22q11.2微重复的个体具有高智力水平的情况,都很引人注目。到目前为止,已经描述了63例对应35个家庭的22q11.2微重复患者。22q11.2微重复可在表型正常/接近正常的个体中出现这一事实此前也有报道。我们推测,目前所描述的临床发现可能是由于确诊偏倚,因为进行22号染色体荧光原位杂交分析最常见的原因是排除微缺失。需要未来的报告来回答微重复是一种非致病性多态性,还是一种具有非常大的临床变异性和低外显率的真正综合征这一问题。