Huang Min, Wang Yanhong, Gu Jingjin, Yang Jing, Noel Karen, Mitchell Beverly S, Schramm Vern L, Graves Lee M
Department of Medicine, Stanford University, Stanford, CA 94305, USA.
Leuk Res. 2008 Aug;32(8):1268-78. doi: 10.1016/j.leukres.2007.12.015. Epub 2008 Feb 14.
Immucillin-H (BCX-1777, forodesine) is a transition state analogue and potent inhibitor of PNP that shows promise as a specific agent against activated human T-cells and T-cell leukemias. The immunosuppressive or antileukemic effects of Immucillin-H (ImmH) in cultured cells require co-administration with deoxyguanosine (dGuo) to attain therapeutic levels of intracellular dGTP. In this study we investigated the requirements for sensitivity and resistance to ImmH and dGuo. (3)H-ImmH transport assays demonstrated that the equilibrative nucleoside transporters (ENT1 and ENT2) facilitated the uptake of ImmH in human leukemia CCRF-CEM cells whereas (3)H-dGuo uptake was primarily dependent upon concentrative nucleoside transporters (CNTs). Analysis of lysates from ImmH-resistant CCRF-CEM-AraC-8D cells demonstrated undetectable deoxycytidine kinase (dCK) activity, suggesting that dCK and not deoxyguanosine kinase (dGK) was the rate-limiting enzyme for phosphorylation of dGuo in these cells. Examination of ImmH cytotoxicity in a hypoxanthine-guanine phosphoribosyltransferase (HGPRT)-deficient cell line CCRF-CEM-AraC-8C, demonstrated enhanced sensitivity to low concentrations of ImmH and dGuo. RT-PCR and sequencing of HGPRT from the HGPRT-deficient CCRF-CEM-AraC-8C cells identified an Exon 8 deletion mutation in this enzyme. Thus these studies show that specific nucleoside transporters are required for ImmH cytotoxicity and predict that ImmH may be more cytotoxic to 6-thioguanine (6-TG) or 6-thiopurine-resistant leukemia cells caused by HGPRT deficiency.
免疫菌素-H(BCX-1777,福多司坦)是嘌呤核苷磷酸化酶(PNP)的过渡态类似物和强效抑制剂,有望成为针对活化的人T细胞和T细胞白血病的特异性药物。免疫菌素-H(ImmH)在培养细胞中的免疫抑制或抗白血病作用需要与脱氧鸟苷(dGuo)共同给药,以达到细胞内dGTP的治疗水平。在本研究中,我们调查了对ImmH和dGuo敏感性和抗性的要求。³H-ImmH转运试验表明,平衡核苷转运体(ENT1和ENT2)促进了人白血病CCRF-CEM细胞对ImmH的摄取,而³H-dGuo的摄取主要依赖于浓缩核苷转运体(CNTs)。对ImmH耐药的CCRF-CEM-AraC-8D细胞裂解物的分析表明,未检测到脱氧胞苷激酶(dCK)活性,这表明dCK而非脱氧鸟苷激酶(dGK)是这些细胞中dGuo磷酸化的限速酶。在次黄嘌呤-鸟嘌呤磷酸核糖转移酶(HGPRT)缺陷细胞系CCRF-CEM-AraC-8C中检测ImmH细胞毒性,结果表明对低浓度的ImmH和dGuo敏感性增强。对HGPRT缺陷的CCRF-CEM-AraC-8C细胞的HGPRT进行RT-PCR和测序,确定该酶存在外显子8缺失突变。因此,这些研究表明,ImmH细胞毒性需要特定的核苷转运体,并预测ImmH对由HGPRT缺陷引起的6-硫鸟嘌呤(6-TG)或6-硫嘌呤耐药白血病细胞可能更具细胞毒性。