Chung Ki Wha, Kim Sang-Beom, Cho Sun Young, Hwang Su Jin, Park Sun Wha, Kang Sung Hee, Kim Joonki, Yoo Jeong Hyun, Choi Byung-Ok
Department of Biological Science, Kongju National University, Gongju, Korea.
Exp Mol Med. 2008 Jun 30;40(3):304-12. doi: 10.3858/emm.2008.40.3.304.
Distal hereditary motor neuropathy (dHMN) is a heterogeneous disorder characterized by degeneration of motor nerves in the absence of sensory abnormalities. Recently, mutations in the small heat shock protein 27 (HSP27) gene were found to cause dHMN type II or Charcot-Marie-Tooth disease type 2F (CMT2F). The authors studied 151 Korean axonal CMT or dHMN families, and found a large Korean dHMN type II family with the Ser135Phe mutation in HSP27. This mutation was inherited in an autosomal dominant manner, and was well associated with familial members with the dHMN phenotype. This mutation site is located in the alpha-crystallin domain and is highly conserved between different species. The frequency of this HSP27 mutation in Koreans was 0.6%. Magnetic resonance imaging analysis revealed that fatty infiltrations tended to progressively extend distal to proximal muscles in lower extremities. In addition, fatty infiltrations in thigh muscles progressed to affect posterior and anterior compartments but to lesser extents in medial compartment, which differs from CMT1A patients presenting with severe involvements of posterior and medial compartments but less involvement of anterior compartment. The authors describe the clinical and neuroimaging findings of the first Korean dHMN patients with the HSP27 Ser135Phe mutation. To our knowledge, this is the first report of the neuroimaging findings of dHMN type II.
远端遗传性运动神经病(dHMN)是一种异质性疾病,其特征为运动神经变性而无感觉异常。最近,发现小热休克蛋白27(HSP27)基因突变可导致II型dHMN或2F型夏科-马里-图斯病(CMT2F)。作者研究了151个韩国轴索性CMT或dHMN家系,发现一个大型韩国II型dHMN家系,其HSP27基因存在Ser135Phe突变。该突变以常染色体显性方式遗传,且与具有dHMN表型的家族成员密切相关。此突变位点位于α-晶状体蛋白结构域,在不同物种间高度保守。该HSP27突变在韩国人中的频率为0.6%。磁共振成像分析显示,脂肪浸润倾向于从下肢肌肉的远端向近端逐渐扩展。此外,大腿肌肉的脂肪浸润进展至影响后肌群和前肌群,但对内侧肌群的影响较小,这与CMT1A患者不同,后者表现为后肌群和内侧肌群严重受累,而前肌群受累较少。作者描述了首例携带HSP27 Ser135Phe突变的韩国dHMN患者的临床和神经影像学表现。据我们所知,这是II型dHMN神经影像学表现的首次报道。