Department of Medical Oncology, CCA 1-38, VU University Medical Center, De Boelelaan 1117, 1081 HV Amsterdam, The Netherlands.
Drug Resist Updat. 2009 Aug-Oct;12(4-5):114-26. doi: 10.1016/j.drup.2009.07.001. Epub 2009 Aug 3.
Multiple molecular, cellular, micro-environmental and systemic causes of anticancer drug resistance have been identified during the last 25 years. At the same time, genome-wide analysis of human tumor tissues has made it possible in principle to assess the expression of critical genes or mutations that determine the response of an individual patient's tumor to drug treatment. Why then do we, with a few exceptions, such as mutation analysis of the EGFR to guide the use of EGFR inhibitors, have no predictive tests to assess a patient's drug sensitivity profile. The problem urges the more with the expanding choice of drugs, which may be beneficial for a fraction of patients only. In this review we discuss recent studies and insights on mechanisms of anticancer drug resistance and try to answer the question: do we understand why a patient responds or fails to respond to therapy? We focus on doxorubicin as example of a classical cytotoxic, DNA damaging agent and on sunitinib, as example of the new generation of (receptor) tyrosine kinase-targeted agents. For both drugs, classical tumor cell autonomous resistance mechanisms, such as drug efflux transporters and mutations in the tumor cell's survival signaling pathways, as well as micro-environment-related resistance mechanisms, such as changes in tumor stromal cell composition, matrix proteins, vascularity, oxygenation and energy metabolism may play a role. Novel agents that target specific mutations in the tumor cell's damage repair (e.g. PARP inhibitors) or that target tumor survival pathways, such as Akt inhibitors, glycolysis inhibitors or mTOR inhibitors, are of high interest. In order to increase the therapeutic index of treatments, fine-tuned synergistic combinations of new and/or classical cytotoxic agents will be designed. More quantitative assessment of potential resistance mechanisms in real tumors and in real time, such as by kinase profiling methodology, will be developed to allow more precise prediction of the optimal drug combination to treat each patient.
在过去的 25 年中,已经确定了多种导致抗癌药物耐药的分子、细胞、微环境和系统性原因。同时,对人类肿瘤组织的全基因组分析使得评估决定个体患者肿瘤对药物治疗反应的关键基因或突变的表达成为可能。那么,为什么除了 EGFR 突变分析指导 EGFR 抑制剂的使用等少数情况外,我们没有预测性测试来评估患者的药物敏感性谱呢?随着可供选择的药物不断增加,这个问题变得更加紧迫,而这些药物可能只对一部分患者有益。在这篇综述中,我们讨论了最近关于抗癌药物耐药机制的研究和见解,并试图回答以下问题:我们是否了解为什么患者对治疗有反应或无反应?我们以阿霉素为例,探讨了经典的细胞毒性、DNA 损伤药物的耐药机制,以舒尼替尼为例,探讨了新一代(受体)酪氨酸激酶靶向药物的耐药机制。对于这两种药物,肿瘤细胞自主耐药机制,如药物外排转运体和肿瘤细胞存活信号通路中的突变,以及与微环境相关的耐药机制,如肿瘤间质细胞组成、基质蛋白、血管生成、氧合和能量代谢的改变,都可能发挥作用。针对肿瘤细胞损伤修复中的特定突变的新型药物(如 PARP 抑制剂)或针对肿瘤存活途径的药物(如 Akt 抑制剂、糖酵解抑制剂或 mTOR 抑制剂)具有很高的研究价值。为了提高治疗的治疗指数,将设计新的和/或经典细胞毒性药物的精细协同组合。将开发更精确的实时评估潜在耐药机制的方法,如激酶谱分析方法,以更精确地预测治疗每个患者的最佳药物组合。