Murphy S, Gorman G, Beetz C, Byrne P, Dytko M, McMonagle P, Kinsella K, Farrell M, Hutchinson M
Department of Neurology, St. Vincent's University Hospital, Elm Park, Dublin 4, Ireland.
Neurology. 2009 Aug 4;73(5):378-84. doi: 10.1212/WNL.0b013e3181b04c6c.
Cognitive impairment and dementia has been reported in autosomal dominant hereditary spastic paraparesis (HSP) linked to the SPG4 locus. There has only been one postmortem examination described; not all accept that progressive cognitive decline is a feature of this disorder.
A family with SPG4-HSP known to have a deletion of exon 17 in the spastin gene (SPG4delEx17) was cognitively assessed over a 7-year period. The index family member died and a postmortem examination was performed.
Thirteen family members older than 40 years were clinically and cognitively assessed using the Cambridge Cognitive Assessment over a 7-year period. The presence of SPG4delEx17 was assessed; a neuropathologic examination of the brain of the index family member was performed.
Cognitive decline occurred in 6 of the 13 family members and in all 4 older than 60 years. Two genetic deletions were identified: SPG4delEx17 in 12 of the 13 family members and a deletion of SPG6 (SPG6del) in 5. Eight individuals had the SPG4delEx17 deletion only; 4 had evidence of progressive cognitive impairment. Four family members had both SPG4delEx17 and SPG6del; 2 of these had cognitive impairment. One family member with the SPG6del alone had neither HSP nor cognitive impairment. The index case with both deletions died with dementia; the brain showed widespread ubiquitin positivity within the neocortex and white matter.
Cognitive decline and dementia is a feature of SPG4-HSP due to a deletion of exon 17 of the spastin gene.
与SPG4基因座相关的常染色体显性遗传性痉挛性截瘫(HSP)中已报道存在认知障碍和痴呆。仅描述过一次尸检;并非所有人都认为进行性认知衰退是该疾病的一个特征。
对一个已知痉挛蛋白基因(SPG4delEx17)外显子17缺失的SPG4 - HSP家族进行了为期7年的认知评估。该家族的索引成员去世后进行了尸检。
在7年时间里,对13名年龄超过40岁的家族成员进行了临床和认知评估,采用剑桥认知评估量表。评估是否存在SPG4delEx17;对索引家族成员的大脑进行了神经病理学检查。
13名家族成员中有6名出现认知衰退,所有4名年龄超过60岁的成员均出现认知衰退。鉴定出两种基因缺失:13名家族成员中有12名存在SPG4delEx17,5名存在SPG6缺失(SPG6del)。8名个体仅存在SPG4delEx17缺失;其中4名有进行性认知障碍的证据。4名家族成员同时存在SPG4delEx17和SPG6del;其中2名有认知障碍。1名仅存在SPG6del的家族成员既没有HSP也没有认知障碍。同时存在两种缺失的索引病例死于痴呆;大脑新皮质和白质内广泛存在泛素阳性。
由于痉挛蛋白基因外显子17缺失,认知衰退和痴呆是SPG4 - HSP的一个特征。