Division of Gastroenterology and Hepatology, Mayo Clinic College of Medicine, 200 First St. SW, Rochester, MN 55905, USA.
Best Pract Res Clin Gastroenterol. 2010 Oct;24(5):647-54. doi: 10.1016/j.bpg.2010.07.006.
Primary biliary cirrhosis (PBC) is an idiopathic chronic autoimmune liver disease that primarily affects women. It is believed that the aetiology for PBC is a combination between environmental triggers in genetically vulnerable persons. The diagnosis for PBC is made when two of the three criteria are fulfilled and they are: (1) biochemical evidence of cholestatic liver disease for at least 6 month's duration; (2) anti-mitochondrial antibody (AMA) positivity; and (3) histologic features of PBC on liver biopsy. Ursodeoxycholic acid (UDCA) is the only FDA-approved medical treatment for PBC and should be administered at a recommended dose of 13-15 mg/kg/day. Unfortunately despite adequate dosing of UDCA, approximately one-third of patients does not respond adequately and may require liver transplantation. Future studies are necessary to elucidate the role of environmental exposures and overall genetic impact not only in the development of PBC, but on disease progression and variable clinical response to therapy.
原发性胆汁性肝硬化(PBC)是一种特发性慢性自身免疫性肝病,主要影响女性。据信,PBC 的病因是遗传易感性个体中环境诱因的组合。当满足以下三个标准中的两个时,即可诊断为 PBC:(1)至少 6 个月的胆汁淤积性肝病的生化证据;(2)抗线粒体抗体(AMA)阳性;(3)肝活检的 PBC 组织学特征。熊去氧胆酸(UDCA)是唯一获得美国食品和药物管理局(FDA)批准的 PBC 治疗药物,应按推荐剂量 13-15mg/kg/天给药。不幸的是,尽管给予了足够剂量的 UDCA,大约三分之一的患者仍不能充分应答,可能需要进行肝移植。未来的研究需要阐明环境暴露和整体遗传影响的作用,不仅在 PBC 的发展中,而且在疾病进展和对治疗的可变临床反应中。