美国食品药品监督管理局的孤儿药管理部门 - Suppr

Orphanage at the FDA.

作者信息

Chen Eric

机构信息

Humanitarian Use Devices Designation Program, Office of Orphan Products Development, Food and Drug Administration, Silver Spring, MD, USA.

出版信息

J Cardiovasc Transl Res. 2012 Oct;5(5):735-6. doi: 10.1007/s12265-010-9242-2. Epub 2010 Nov 16.

DOI:10.1007/s12265-010-9242-2

PMID:21080134

Abstract

摘要

相似文献

Orphanage at the FDA.

J Cardiovasc Transl Res. 2012 Oct;5(5):735-6. doi: 10.1007/s12265-010-9242-2. Epub 2010 Nov 16.

Regulators adopt more orphan drugs.

Nature. 2014 Apr 3;508(7494):16-7. doi: 10.1038/508016a.

Raising orphans: how clinical development programs of drugs for rare and common diseases are different.

Clin Pharmacol Ther. 2012 Aug;92(2):262-4. doi: 10.1038/clpt.2012.87. Epub 2012 Jun 27.

[Orphan drugs: drugs for rare diseases].

Dtsch Med Wochenschr. 2010 May;135(18):p17.

A personal perspective of orphan drug development for rare diseases: A golden opportunity or an unsustainable future?

J Clin Pharmacol. 2016 Mar;56(3):257-9. doi: 10.1002/jcph.599. Epub 2015 Sep 18.

Rare diseases, orphan drugs and their regulation: questions and misconceptions.

Nat Rev Drug Discov. 2010 Dec;9(12):921-9. doi: 10.1038/nrd3275. Epub 2010 Nov 9.

The Orphan Drug Act Revisited.

JAMA. 2019 Mar 5;321(9):833-834. doi: 10.1001/jama.2019.0290.

Orphan drug development: an economically viable strategy for biopharma R&D.

Drug Discov Today. 2012 Jul;17(13-14):660-4. doi: 10.1016/j.drudis.2012.02.005. Epub 2012 Feb 17.

Medicines for rare (orphan) diseases: an enquiry and proposal for tax-incentives.

Drug Discov Today. 2011 Dec;16(23-24):999-1000. doi: 10.1016/j.drudis.2011.10.004. Epub 2011 Oct 14.

Duel over discounts. Pharma, providers at odds over 'orphan drugs'.

Mod Healthc. 2012 Jan 23;42(4):30-1.

引用本文的文献

Between hope and reality: treatment of genetic diseases through nucleic acid-based drugs.

Commun Biol. 2024 Apr 23;7(1):489. doi: 10.1038/s42003-024-06121-9.

文献AI研究员

20分钟写一篇综述，助力文献阅读效率提升50倍。

立即体验

用中文搜PubMed

大模型驱动的PubMed中文搜索引擎

马上搜索

文档翻译

学术文献翻译模型，支持多种主流文档格式。

立即体验

相似文献

Orphanage at the FDA.

J Cardiovasc Transl Res. 2012 Oct;5(5):735-6. doi: 10.1007/s12265-010-9242-2. Epub 2010 Nov 16.

Regulators adopt more orphan drugs.

Nature. 2014 Apr 3;508(7494):16-7. doi: 10.1038/508016a.

Raising orphans: how clinical development programs of drugs for rare and common diseases are different.

Clin Pharmacol Ther. 2012 Aug;92(2):262-4. doi: 10.1038/clpt.2012.87. Epub 2012 Jun 27.

[Orphan drugs: drugs for rare diseases].

Dtsch Med Wochenschr. 2010 May;135(18):p17.

A personal perspective of orphan drug development for rare diseases: A golden opportunity or an unsustainable future?

J Clin Pharmacol. 2016 Mar;56(3):257-9. doi: 10.1002/jcph.599. Epub 2015 Sep 18.

Rare diseases, orphan drugs and their regulation: questions and misconceptions.

Nat Rev Drug Discov. 2010 Dec;9(12):921-9. doi: 10.1038/nrd3275. Epub 2010 Nov 9.

The Orphan Drug Act Revisited.

JAMA. 2019 Mar 5;321(9):833-834. doi: 10.1001/jama.2019.0290.

Orphan drug development: an economically viable strategy for biopharma R&D.

Drug Discov Today. 2012 Jul;17(13-14):660-4. doi: 10.1016/j.drudis.2012.02.005. Epub 2012 Feb 17.

Medicines for rare (orphan) diseases: an enquiry and proposal for tax-incentives.

Drug Discov Today. 2011 Dec;16(23-24):999-1000. doi: 10.1016/j.drudis.2011.10.004. Epub 2011 Oct 14.

Duel over discounts. Pharma, providers at odds over 'orphan drugs'.

Mod Healthc. 2012 Jan 23;42(4):30-1.

引用本文的文献

Between hope and reality: treatment of genetic diseases through nucleic acid-based drugs.

Commun Biol. 2024 Apr 23;7(1):489. doi: 10.1038/s42003-024-06121-9.

Orphanage at the FDA.

作者信息

机构信息

出版信息

相似文献

引用本文的文献

文献AI研究员

用中文搜PubMed

文档翻译

Suppr 超能文献

相似文献

引用本文的文献

Orphanage at the FDA.

作者信息

机构信息

出版信息