Department of Ophthalmology, the First Affiliated Hospital, School of Medicine, Zhejiang University, Hangzhou, China.
J Zhejiang Univ Sci B. 2011 Apr;12(4):287-92. doi: 10.1631/jzus.B1000154.
In this paper, we report the clinical and molecular features of the distinct TGFBI (human transforming growth factor β-induced, OMIM No. 601692) gene-linked corneal dystrophy. Altogether, five pedigrees and ten unrelated individuals diagnosed as corneal dystrophy were recruited. Peripheral venous DNA was extracted, and then amplified by polymerase chain reaction (PCR) and scanned for mutation by single-stranded conformation polymorphism (SSCP). Direct DNA sequencing was used to analyze the mutations of the TGFBI gene. In our study, thirty patients from five pedigrees and ten sporadic patients were diagnosed as four TGFBI gene-linked corneal dystrophies of granular corneal dystrophy type I (GGCD I), Avellino corneal dystrophy (ACD), lattice corneal dystrophy type I (LCD I), and lattice corneal dystrophy type IIIA (LCD IIIA), and in total, seven disease-causing mutations, namely R555W, A546D, A546T, and T538P mutations in exon 12, R124H and R124C mutations in exon 4, and P501T mutation in exon 11, were identified, while four polymorphisms of V327V, L472L, F540F, and 1665-1666insC were screened in exons 8, 11, and 12. The study ascertained the tight genotype-phenotype relationship and confirmed the clinical and genetic features of four TGFBI gene-linked corneal dystrophies.
本文报道了 TGFBI(人类转化生长因子 β 诱导,OMIM No.601692)基因相关角膜营养不良的临床和分子特征。共招募了五个家系和十个无关个体,诊断为角膜营养不良。提取外周静脉 DNA,然后通过聚合酶链反应(PCR)扩增并通过单链构象多态性(SSCP)扫描突变。直接 DNA 测序用于分析 TGFBI 基因突变。在本研究中,来自五个家系的三十名患者和十个散发病例被诊断为四种 TGFBI 基因相关的角膜营养不良,即颗粒状角膜营养不良 I 型(GGCD I)、阿维里诺角膜营养不良(ACD)、格子状角膜营养不良 I 型(LCD I)和格子状角膜营养不良 IIIA 型(LCD IIIA),共鉴定出七个致病突变,即外显子 12 中的 R555W、A546D、A546T 和 T538P 突变,外显子 4 中的 R124H 和 R124C 突变,以及外显子 11 中的 P501T 突变,同时在外显子 8、11 和 12 中筛选出四个多态性 V327V、L472L、F540F 和 1665-1666insC。该研究确定了紧密的基因型-表型关系,并证实了四种 TGFBI 基因相关角膜营养不良的临床和遗传特征。