Department of Pediatrics, Saint Mary's Hospital, Luodong, Taiwan.
Pediatr Nephrol. 2011 Oct;26(10):1903-7. doi: 10.1007/s00467-011-1918-6. Epub 2011 May 26.
We try to explain why hypercalciuria is absent at diagnosis in some children with an ATP6V1B1 mutation. A 5-month-old girl presented with distal renal tubular acidosis (dRTA) and sensorineural hearing loss. Direct sequencing of the ATP6V1B1 genes disclosed a new homozygous mutation (452 delT) in exon 13. In particular, an absence of hypercalciuria and a normal level of parathyroid hormones were noted. After alkaline therapy, the signs of nephrocalcinosis improved on ultrasound during follow-up. After a review of the literature regarding patients with ATP6V1B1 gene mutations, a young age seemed to be an important factor for normocalciuria. The probable mechanism of normocalciuria and a dynamic mode of calcium excretion in patients with dRTA is proposed. The determinant factors include the degree of systemic acidosis, urine pH, genetic polymorphisms, age, dietary factors, and volume status. Low sodium intake may be a major determinant of normocalciuria in these patients. It is suggested that hypercalciuria is usually absent at diagnosis of dRTA in young infants. Blood pH, plasma bicarbonate concentration, urinary citrate levels, and growth catch-up may be better indicators of adequate alkali therapy in normocalciuric children. Volume contraction, low salt content in infant formula, and alkaline urine in young infants are likely to account for the increased calcium reabsorption.
我们试图解释为什么在一些患有 ATP6V1B1 突变的儿童中,在诊断时没有出现高钙尿症。一名 5 个月大的女孩因远端肾小管酸中毒(dRTA)和感觉神经性听力损失就诊。ATP6V1B1 基因的直接测序显示第 13 外显子中有一个新的纯合突变(452delT)。特别是,注意到没有高钙尿症和甲状旁腺激素水平正常。碱性治疗后,在随访期间超声检查发现肾钙质沉着症的迹象有所改善。在回顾了有关 ATP6V1B1 基因突变患者的文献后,年龄较小似乎是正常钙尿症的一个重要因素。提出了 dRTA 患者正常钙尿症和钙排泄动态模式的可能机制。决定因素包括全身酸中毒的程度、尿 pH 值、遗传多态性、年龄、饮食因素和容量状态。低钠摄入可能是这些患者正常钙尿症的主要决定因素。建议在年轻婴儿 dRTA 的诊断时通常没有高钙尿症。血 pH 值、血浆碳酸氢盐浓度、尿柠檬酸盐水平和生长追赶可能是正常钙尿儿童碱治疗充分的更好指标。容量收缩、婴儿配方奶粉中盐含量低以及婴幼儿碱性尿可能导致钙重吸收增加。