Jiang Jingwen, Li Jing, Liu Wenjun
School of Life Sciences, University of Science and Technology of China, Hefei 230027, China
Sheng Wu Gong Cheng Xue Bao. 2011 May;27(5):724-9.
Interest in rare diseases research and orphan drugs development has been increased distinctly in recent years. The number of affected people with rare diseases is considerable around the world and the formulation of national and international incentive policies to accelerate orphan drugs development, aiming at offering facilities and necessary conditions for patient access to treatment, gains favorable results. In particular, more measures should be taken to catalyze further progress due to behindhand level in this field in China. Additionally, therapeutic methods of rare diseases were also discussed.
近年来，对罕见病研究和孤儿药开发的兴趣明显增加。全球范围内，患罕见病的人数相当可观，制定国家和国际激励政策以加速孤儿药开发，旨在为患者获得治疗提供便利和必要条件，已取得良好成效。特别是在中国，由于该领域水平相对滞后，应采取更多措施以推动进一步发展。此外，还讨论了罕见病的治疗方法。
