Section of Genetics, Leeds Institute of Molecular Medicine, St. James's University Hospital, Wellcome Trust Brenner Building, UK.
Am J Hum Genet. 2011 Sep 9;89(3):451-8. doi: 10.1016/j.ajhg.2011.08.002. Epub 2011 Sep 1.
Familial biparental hydatidiform mole (FBHM) is the only known pure maternal-effect recessive inherited disorder in humans. Affected women, although developmentally normal themselves, suffer repeated pregnancy loss because of the development of the conceptus into a complete hydatidiform mole in which extraembryonic trophoblastic tissue develops but the embryo itself suffers early demise. This developmental phenotype results from a genome-wide failure to correctly specify or maintain a maternal epigenotype at imprinted loci. Most cases of FBHM result from mutations of NLRP7, but genetic heterogeneity has been demonstrated. Here, we report biallelic mutations of C6orf221 in three families with FBHM. The previously described biological properties of their respective gene families suggest that NLRP7 and C6orf221 may interact as components of an oocyte complex that is directly or indirectly required for determination of epigenetic status on the oocyte genome.
家族性双父性葡萄胎(FBHM)是人类唯一已知的纯母性效应隐性遗传疾病。受影响的女性本身发育正常,但由于胚胎发育成完全的葡萄胎,胚胎外滋养层组织发育,但胚胎本身早期死亡,她们会反复流产。这种发育表型是由于基因组范围内未能正确指定或维持印迹基因座的母体表型所致。大多数 FBHM 病例是由 NLRP7 突变引起的,但已证明存在遗传异质性。在这里,我们报告了三个 FBHM 家族中 C6orf221 的双等位基因突变。其各自基因家族先前描述的生物学特性表明,NLRP7 和 C6orf221 可能作为卵母细胞复合物的组成部分相互作用,该复合物直接或间接地需要确定卵母细胞基因组上的表观遗传状态。