Origone Paola, Caponnetto Claudia, Mantero Vittorio, Cichero Elena, Fossa Paola, Geroldi Alessandro, Verdiani Simonetta, Bellone Emilia, Mancardi Gianluigi, Mandich Paola
Department of Biology and Genetics, University of Genoa and U.O.C. Medical Genetics of Azienda Ospedaliera Universitaria S. Martino di Genova, Genoa, Italy.
Amyotroph Lateral Scler. 2012 Jan;13(1):144-8. doi: 10.3109/17482968.2011.614254. Epub 2011 Sep 19.
In this report we describe a novel SOD1 mutation (Gly147Ser) in an Italian sporadic ALS patient. The patient presented with hoarseness due to bilateral vocal cord paralysis and a rapid clinical course. Mutational analysis of the SOD1 gene was carried out by direct sequencing. In silico bioinformatics analysis and molecular modelling was used to analyse the SOD1 function modifications produced by the mutated residue. A heterozygous c.442 G > A transition, which leads to a change at codon 147 resulting in a serine rather than glycine, was found in the patient. Bioinformatics analysis and molecular modelling strongly suggest a dramatic effect of Gly147Ser mutation on SOD1 function. In conclusion, Gly147Ser represent a new missense mutation whose effect may correlate with the peculiar clinical bulbar phenotype onset with bilateral vocal cord paresis and rapid clinical course of the disease. Ethical and psychological dilemmas about genetic testing in apparently sporadic subjects are still matter of debate.