基因治疗的临床进展：严重B型血友病患者出血性疾病的持续部分纠正。 - Suppr

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超能文献

Clinical progress in gene therapy: sustained partial correction of the bleeding disorder in patients suffering from severe hemophilia B.

作者信息

Vandendriessche T, Chuah M K

机构信息

Department of Gene Therapy & Regenerative Medicine, Free University of Brussels (VUB) , B-1090 Brussels, Belgium.

出版信息

Hum Gene Ther. 2012 Jan;23(1):4-6. doi: 10.1089/hum.2011.221.

DOI:10.1089/hum.2011.221

PMID:22149214

Abstract

摘要

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相似文献

Clinical progress in gene therapy: sustained partial correction of the bleeding disorder in patients suffering from severe hemophilia B.

Hum Gene Ther. 2012 Jan;23(1):4-6. doi: 10.1089/hum.2011.221.

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Mol Ther. 2017 May 3;25(5):1163-1167. doi: 10.1016/j.ymthe.2017.03.033. Epub 2017 Apr 11.

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Int J Hematol. 2020 Jan;111(1):31-41. doi: 10.1007/s12185-018-2513-4. Epub 2018 Aug 6.

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Semin Thromb Hemost. 2000;26(2):179-88. doi: 10.1055/s-2000-9821.

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