反义疗法治疗脊髓性肌萎缩症的意义。 - Suppr

Suppr

超能文献

Sense in antisense therapy for spinal muscular atrophy.

作者信息

MacKenzie Alex

机构信息

Children's Hospital of Eastern Ontario and the University of Ottawa, Ottawa.

出版信息

N Engl J Med. 2012 Feb 23;366(8):761-3. doi: 10.1056/NEJMcibr1114629.

DOI:10.1056/NEJMcibr1114629

PMID:22356331

Abstract

摘要

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