Department of Medical Genetics, Genome-Scale Biology Research Program, University of Helsinki, Helsinki, Finland.
Hum Reprod. 2012 Jun;27(6):1865-9. doi: 10.1093/humrep/des105. Epub 2012 Apr 3.
Hereditary leiomyomatosis and renal cell cancer (HLRCC) is a tumor predisposition syndrome characterized by cutaneous and uterine leiomyomas and renal cell cancer. HLRCC is caused by heterozygous germline mutations in the fumarate hydratase (FH) gene. A Finnish family with nine closely related women with uterine leiomyomas was detected by an alert gynecologist. No cutaneous or renal cell tumors were reported in the family when it was referred to genetic analyses. Samples were available from seven patients, and a novel germline FH mutation was detected in five of them. Mutation carriers were symptomatic, had multiple tumors and were diagnosed at an early age. This study emphasizes the importance of considering FH mutation screening when gynecologists encounter families with multiple severe uterine leiomyoma cases. Due to possibility of phenocopies more than one patient should be tested. Early mutation detection allows regular screening of the mutation carriers and enables early detection of possible highly aggressive renal tumors. It may also affect family planning as multiple myomas at early age may significantly reduce fertility.
遗传性平滑肌瘤病和肾细胞癌(HLRCC)是一种肿瘤易感性综合征,其特征为皮肤和子宫平滑肌瘤以及肾细胞癌。HLRCC 是由延胡索酸水合酶(FH)基因的杂合胚系突变引起的。一位警觉的妇科医生发现了一个芬兰家族,该家族中有 9 位密切相关的女性患有子宫平滑肌瘤。当该家族被转介进行基因分析时,并未报告有皮肤或肾细胞肿瘤。从 7 名患者中获得了样本,并在其中 5 名患者中检测到了一种新的 FH 种系突变。突变携带者有症状,有多发性肿瘤,且在年轻时被诊断出。这项研究强调了妇科医生在遇到多个严重子宫平滑肌瘤病例的家族时,考虑进行 FH 突变筛查的重要性。由于存在表型模拟的可能性,不止一位患者应该接受检测。早期突变检测可允许对突变携带者进行定期筛查,并能够早期发现可能具有高度侵袭性的肾肿瘤。它还可能影响计划生育,因为年轻时多发性肌瘤可能会显著降低生育能力。