神经退行性疾病：建立亨廷顿病的临床试验电池。
Neurodegenerative disease: Establishing a clinical trial battery for Huntington disease.
出版信息
Nat Rev Neurol. 2012 Apr 10;8(5):250-1. doi: 10.1038/nrneurol.2012.67.
Abstract
The success of clinical trials in Huntington disease (HD) will depend to a large degree on the quality of the outcome measures. Using data from the TRACK-HD study, a recent publication proposes a battery of assessments that could be used as outcomes in future clinical trials in patients with early HD.
摘要
亨廷顿病（HD）临床试验的成功在很大程度上取决于结局测量的质量。利用 TRACK-HD 研究的数据，最近的一篇出版物提出了一系列评估方法，这些方法可以作为早期 HD 患者未来临床试验的结局指标。
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本文引用的文献
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