Division of Pediatric Gastroenterology, Hepatology and Nutrition, Department of Pediatrics, University of Pittsburgh School of Medicine, Pittsburgh, PA, USA.
J Lipid Res. 2013 Feb;54(2):379-85. doi: 10.1194/jlr.M030304. Epub 2012 Dec 4.
Functional defects in ATPase class I type 8B membrane 1 (ATP8B1 or familial intrahepatic cholestasis 1, FIC1) lead to cholestasis by mechanism(s) that are not fully understood. One proposed pathophysiology involves aberrant signaling to the bile acid sensor, the farnesoid X receptor (FXR), via protein kinase C ζ (PKCζ). The following cell line-based studies investigated whether phospholipase D2 may transduce a signal from FIC1 to FXR. PLD2 gain of function led to activation of the bile salt export pump (BSEP) promoter, a well-characterized FXR response. BSEP activation by PLD2 could be blocked by abrogating either PKCζ or FXR signaling. PLD2 loss of function led to a reduction in BSEP promoter activity. In addition, a variety of proteins that are activated by FXR, including BSEP, were reduced in HepG2 cells treated with PLD2 siRNA. Similar effects were observed in freshly isolated human hepatocytes. Activation of BSEP by FIC1 gain of function was blocked when PLD2 but not PLD1 was silenced. Overexpression of wild-type but not Byler mutant FIC1 led to an increase in membrane associated PLD activity. An intermediate level of activation of PLD activity was induced when a benign recurrent intrahepatic cholestasis FIC1 mutant construct was expressed. These studies show that FIC1 signals to FXR via a signaling pathway including PLD2 and PKCζ.
ATP 酶 I 类 8B 膜 1(ATP8B1 或家族性肝内胆汁淤积症 1,FIC1)的功能缺陷导致胆汁淤积的机制尚不完全清楚。一种提出的病理生理学涉及异常信号到胆汁酸传感器,法尼醇 X 受体(FXR),通过蛋白激酶 C ζ(PKCζ)。以下基于细胞系的研究调查了磷脂酶 D2 是否可以从 FIC1 向 FXR 转导信号。PLD2 功能获得导致胆汁盐输出泵(BSEP)启动子的激活,这是 FXR 反应的一个很好的特征。通过 PLD2 激活 BSEP 可以通过废除 PKCζ 或 FXR 信号来阻断。PLD2 功能丧失导致 BSEP 启动子活性降低。此外,在用 PLD2 siRNA 处理的 HepG2 细胞中,多种被 FXR 激活的蛋白质,包括 BSEP,减少。在新鲜分离的人肝细胞中也观察到类似的效果。当沉默 PLD2 而不是 PLD1 时,FIC1 功能获得激活 BSEP 的作用被阻断。野生型但不是 Byler 突变 FIC1 的过表达导致膜相关 PLD 活性增加。当表达良性复发性肝内胆汁淤积症 FIC1 突变构建体时,诱导 PLD 活性的中间水平激活。这些研究表明,FIC1 通过包括 PLD2 和 PKCζ 的信号通路向 FXR 发出信号。