Department of Neurology, University of Pennsylvania and the Children's Hospital of Philadelphia, Philadelphia, Pennsylvania 19104, USA.
Mov Disord. 2013 Feb;28(2):190-5. doi: 10.1002/mds.25201. Epub 2012 Dec 12.
To reduce study start-up time, increase data sharing, and assist investigators conducting clinical studies, the National Institute of Neurological Disorders and Stroke embarked on an initiative to create common data elements for neuroscience clinical research. The Common Data Element Team developed general common data elements, which are commonly collected in clinical studies regardless of therapeutic area, such as demographics. In the present project, we applied such approaches to data collection in Friedreich's ataxia (FRDA), a neurological disorder that involves multiple organ systems. To develop FRDA common data elements, FRDA experts formed a working group and subgroups to define elements in the following: ataxia and performance measures; biomarkers; cardiac and other clinical outcomes; and demographics, laboratory tests, and medical history. The basic development process included identification of international experts in FRDA clinical research, meeting by teleconference to develop a draft of standardized common data elements recommendations, vetting of recommendations across the subgroups, and dissemination of recommendations to the research community for public comment. The full recommendations were published online in September 2011 at http://www.commondataelements.ninds.nih.gov/FA.aspx. The subgroups' recommendations are classified as core, supplemental, or exploratory. Template case report forms were created for many of the core tests. The present set of data elements should ideally lead to decreased initiation time for clinical research studies and greater ability to compare and analyze data across studies. Their incorporation into new, ongoing studies will be assessed in an ongoing fashion to define their utility in FRDA.
为了减少研究启动时间、增加数据共享并协助进行临床研究的调查员,国家神经疾病与中风研究所启动了一项计划,旨在为神经科学临床研究创建通用数据元素。通用数据元素团队制定了一般通用数据元素,这些元素是临床研究中无论治疗领域如何都通常收集的,例如人口统计学信息。在本项目中,我们将这些方法应用于弗里德里希共济失调症(FRDA)的数据收集,这是一种涉及多个器官系统的神经疾病。为了制定 FRDA 通用数据元素,FRDA 专家组成了一个工作组和子组,以定义以下方面的元素:共济失调和表现测量、生物标志物、心脏和其他临床结果以及人口统计学、实验室测试和病史。基本的开发过程包括确定 FRDA 临床研究的国际专家,通过电话会议开会制定标准化通用数据元素建议草案,对子组的建议进行审查,并将建议分发给研究界供公众评论。完整的建议于 2011 年 9 月在 http://www.commondataelements.ninds.nih.gov/FA.aspx 上在线发布。子组的建议被分类为核心、补充或探索性。许多核心测试都创建了模板病例报告表。这组数据元素理想情况下应该可以减少临床研究启动时间,并增强跨研究比较和分析数据的能力。将其纳入新的正在进行的研究将以持续的方式进行评估,以确定其在 FRDA 中的实用性。