Nishiwaki S, Atsuta Y, Tanaka J
Department of Hematology and Oncology, Nagoya University Graduate School of Medicine, Nagoya, Japan.
Bone Marrow Transplant. 2013 Nov;48(11):1369-76. doi: 10.1038/bmt.2013.20. Epub 2013 Mar 11.
The best outcome for patients with Ph chromosome-negative ALL (Ph(-) ALL) can be obtained by HLA-matched related donor (mRD) allogeneic hematopoietic cell transplantation (allo-HCT) in first CR. However, only 30% of patients have a mRD. Three alternative sources, unrelated donor (URD), cord blood, and haploidentical related donor (haplo-RD), are available. URD allo-HCT is an old-established alternative source, and recent data have shown that URD allo-HCT can result in OS comparable with that with mRD allo-HCT for patients with Ph(-) ALL in first CR (OS at 4 years: mRD 65% vs URD 62%). Unrelated cord blood transplantation can also be indicated for patients with Ph(-) ALL in first CR (OS at 4 years: 57%), especially for young patients without an HLA-matched URD or patients who are in urgent need for allo-HCT. Limited data for haplo-RD allo-HCT for ALL showed utility in CR (OS at 3 years: up to 65%) but a survival rate of only 5-7% in non-CR. As there are no confirmed data about the utility of allo-HCT from an alternative source for adolescent and young adults who are eligible for pediatric protocols or for elderly patients with reduced-intensity conditioning. Further investigation, including investigation of minimal residual disease detection, may reveal subgroups of patients who can receive benefits from allo-HCT. Selection of the best source based on the patient status and appropriate timing is warranted.
对于Ph染色体阴性急性淋巴细胞白血病(Ph(-) ALL)患者,在首次完全缓解(CR)时通过人类白细胞抗原(HLA)匹配的相关供者(mRD)进行异基因造血细胞移植(allo-HCT)可获得最佳疗效。然而,只有30%的患者有mRD。还有三种替代供者来源可供选择,即无关供者(URD)、脐血和单倍体相合相关供者(haplo-RD)。URD allo-HCT是一种已确立的替代供者来源,最近的数据表明,对于首次CR的Ph(-) ALL患者,URD allo-HCT的总生存期(OS)与mRD allo-HCT相当(4年OS:mRD为65%,URD为62%)。无关脐血移植也可用于首次CR的Ph(-) ALL患者(4年OS:57%),特别是对于没有HLA匹配的URD的年轻患者或急需allo-HCT的患者。关于ALL的haplo-RD allo-HCT的有限数据显示在CR中有一定作用(3年OS:高达65%),但在非CR患者中的生存率仅为5-7%。由于对于符合儿童方案的青少年和年轻成人或采用减低强度预处理的老年患者,尚无关于替代供者来源allo-HCT效用的确切数据。进一步的研究,包括微小残留病检测的研究,可能会揭示能从allo-HCT中获益的患者亚组。根据患者状况选择最佳供者来源并把握合适时机是必要的。