Department of Cell Pathology, Graduate School of Medical Sciences, Kumamoto University, Kumamoto, Japan.
Pathol Int. 2013 May;63(5):260-5. doi: 10.1111/pin.12055.
Hepatocyte-derived mutant amyloidogenic transthyretin (ATTR) causes familial amyloidotic polyneuropathy (FAP), for which orthotopic liver transplantation is an established curative treatment. However, some patients with FAP have cardiac amyloidosis after transplantation. Here, we describe a man with an autonomic disorder diagnosed as FAP ATTR Val30Met and marked cardiomegaly after liver transplantation. He underwent orthotopic liver transplantation at 49 years of age and was prescribed prednisolone to prevent graft rejection. Two years later, autonomic dysfunction and severe heart failure gradually developed. He died suddenly at 59. The autopsy revealed marked cardiomegaly (heart weight: 1020 g). Histological and ultrastructural examinations demonstrated massive amyloid deposition and unusual myocardial hypertrophic injury associated with nuclear translocation of the glucocorticoid receptor (GR). No other FAP patients without heart failure showed GR nuclear translocation. GR is a nuclear transcription factor that leads to myocardial hypertrophy, and cumulative prednisolone doses may promote marked cardiomegaly and severe cardiac amyloidosis.
肝细胞衍生的突变淀粉样转甲状腺素蛋白 (ATTR) 可导致家族性淀粉样多神经病 (FAP),为此,原位肝移植是一种已确立的治疗方法。然而,一些 FAP 患者在移植后会出现心脏淀粉样变性。在这里,我们描述了一名患有自主神经障碍的男子,其被诊断为 FAP ATTR Val30Met,且在肝移植后出现明显的心脏扩大。他在 49 岁时接受了原位肝移植,并服用泼尼松龙以预防移植物排斥反应。两年后,自主神经功能障碍和严重心力衰竭逐渐出现。他在 59 岁时突然去世。尸检显示明显的心脏扩大(心脏重量:1020 克)。组织学和超微结构检查显示大量淀粉样物质沉积和不寻常的心肌肥厚损伤,伴有糖皮质激素受体 (GR) 的核转位。没有其他没有心力衰竭的 FAP 患者显示 GR 核转位。GR 是一种核转录因子,可导致心肌肥厚,累积泼尼松龙剂量可能会导致明显的心脏扩大和严重的心脏淀粉样变性。