Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America.
PLoS One. 2013 Nov 26;8(11):e80408. doi: 10.1371/journal.pone.0080408. eCollection 2013.
The study of mouse hearing impairment mutants has led to the identification of a number of human hearing impairment genes and has greatly furthered our understanding of the physiology of hearing. The novel mouse mutant neurological/sensory 5 (nse5) demonstrates a significantly reduced or absent startle response to sound and is therefore a potential murine model of human hearing impairment. Genetic analysis of 500 intercross progeny localized the mutant locus to a 524 kilobase (kb) interval on mouse chromosome 15. A missense mutation in a highly-conserved amino acid was found in the asparagine-linked glycosylation 10B gene (Alg10b), which is within the critical interval for the nse5 mutation. A 20.4 kb transgene containing a wildtype copy of the Alg10b gene rescued the mutant phenotype in nse5/nse5 homozygous animals, confirming that the mutation in Alg10b is responsible for the nse5/nse5 mutant phenotype. Homozygous nse5/nse5 mutants had abnormal auditory brainstem responses (ABRs), distortion product otoacoustic emissions (DPOAEs), and cochlear microphonics (CMs). Endocochlear potentials (EPs), on the other hand, were normal. ABRs and DPOAEs also confirmed the rescue of the mutant nse5/nse5 phenotype by the wildtype Alg10b transgene. These results suggested a defect in the outer hair cells of mutant animals, which was confirmed by histologic analysis. This is the first report of mutation in a gene involved in the asparagine (N)-linked glycosylation pathway causing nonsyndromic hearing impairment, and it suggests that the hearing apparatus, and the outer hair cells in particular, are exquisitely sensitive to perturbations of the N-linked glycosylation pathway.
对小鼠听力障碍突变体的研究导致了一些人类听力障碍基因的鉴定,并极大地促进了我们对听力生理学的理解。新型小鼠突变体神经/感觉 5(nse5)表现出对声音的明显减少或缺乏惊吓反应,因此是人类听力障碍的潜在小鼠模型。对 500 个杂交后代的遗传分析将突变体基因座定位到小鼠 15 号染色体上的 524 千碱基(kb)区间。在 Alg10b 基因(Alg10b)中发现了一个高度保守的氨基酸的错义突变,该基因位于 nse5 突变的关键区间内。一个包含 Alg10b 基因野生型拷贝的 20.4 kb 转基因可挽救 nse5/nse5 纯合子动物的突变表型,证实了 Alg10b 突变是 nse5/nse5 突变表型的原因。nse5/nse5 纯合子突变体的听觉脑干反应(ABR)、畸变产物耳声发射(DPOAE)和耳蜗微音(CM)异常。另一方面,内淋巴电位(EP)正常。ABR 和 DPOAE 也证实了野生型 Alg10b 转基因对突变 nse5/nse5 表型的挽救。这些结果表明突变动物的外毛细胞存在缺陷,组织学分析证实了这一点。这是第一个报道参与天冬酰胺(N)连接糖基化途径的基因突变导致非综合征性听力障碍的报告,这表明听力器官,特别是外毛细胞,对外源 N 连接糖基化途径的干扰非常敏感。