Division of Preclinical Innovation, National Institutes of Health Chemical Genomics Center, National Center for Advancing Translational Sciences, Metabolism Branch, Center for Cancer Research, and Developmental Therapeutics Program, Division of Cancer Treatment and Diagnosis, National Cancer Institute, National Institutes of Health, Bethesda, MD 20892.
Proc Natl Acad Sci U S A. 2014 Feb 11;111(6):2349-54. doi: 10.1073/pnas.1311846111. Epub 2014 Jan 27.
The clinical development of drug combinations is typically achieved through trial-and-error or via insight gained through a detailed molecular understanding of dysregulated signaling pathways in a specific cancer type. Unbiased small-molecule combination (matrix) screening represents a high-throughput means to explore hundreds and even thousands of drug-drug pairs for potential investigation and translation. Here, we describe a high-throughput screening platform capable of testing compounds in pairwise matrix blocks for the rapid and systematic identification of synergistic, additive, and antagonistic drug combinations. We use this platform to define potential therapeutic combinations for the activated B-cell-like subtype (ABC) of diffuse large B-cell lymphoma (DLBCL). We identify drugs with synergy, additivity, and antagonism with the Bruton's tyrosine kinase inhibitor ibrutinib, which targets the chronic active B-cell receptor signaling that characterizes ABC DLBCL. Ibrutinib interacted favorably with a wide range of compounds, including inhibitors of the PI3K-AKT-mammalian target of rapamycin signaling cascade, other B-cell receptor pathway inhibitors, Bcl-2 family inhibitors, and several components of chemotherapy that is the standard of care for DLBCL.
药物组合的临床开发通常是通过反复试验或通过对特定癌症类型中失调信号通路的详细分子理解而获得的。无偏小分子组合(矩阵)筛选代表了一种高通量的方法,可以探索数百甚至数千种药物-药物对,以寻找潜在的研究和转化机会。在这里,我们描述了一种高通量筛选平台,能够在成对的矩阵块中测试化合物,以快速系统地鉴定协同、相加和拮抗的药物组合。我们使用该平台来确定激活 B 细胞样亚型(ABC)弥漫性大 B 细胞淋巴瘤(DLBCL)的潜在治疗组合。我们鉴定了与 Bruton 的酪氨酸激酶抑制剂伊布替尼具有协同作用、相加作用和拮抗作用的药物,伊布替尼靶向特征为 ABC DLBCL 的慢性活跃 B 细胞受体信号。伊布替尼与广泛的化合物相互作用良好,包括 PI3K-AKT-雷帕霉素哺乳动物靶标信号级联的抑制剂、其他 B 细胞受体途径抑制剂、Bcl-2 家族抑制剂以及用于 DLBCL 的标准治疗的几种化疗成分。