Amado Marta, Calado Maria Angelina, Ferreira Rui, Lourenço Teresa
Department of Pediatrics, Hospital Unit of Portimão, Centro Hospitalar do Algarve, Portimão, Portugal.
Department of Cardiology, Unit of Pediatric Cardiology, Hospital Dr. Nélio Mendonça, Funchal, Portugal.
BMJ Case Rep. 2014 Jun 13;2014:bcr2013202438. doi: 10.1136/bcr-2013-202438.
Marfan syndrome (MFS) is a genetic disorder of the connective tissue which rarely manifests in the neonatal period and has an ominous prognosis. A case of a first female offspring of healthy parents is described here. The pregnancy was uneventful and the mother had a term caesarean delivery. At birth, some dysmorphic signs became apparent, such as loose redundant skin, dolichocephaly, frontal bossing, deeply sunken eyes, micrognathia, contractures of the elbows, arachnodactyly and hip dysplasia. The echocardiogram showed a mitral and tricuspid valve regurgitation and a long aortic arch. The diagnosis of neonatal MFS came forward and genetic studies revealed a de novo mutation in the fibrillin 1 (FBN1) gene. At 6 months, due to a progressive worsening of the cardiac pathology, she was submitted to mitral valvuloplasty. She is now 2 years and 10 months old, which is a remarkable feat for a child suffering from this condition.
马凡综合征(MFS)是一种结缔组织的遗传性疾病,在新生儿期很少出现,预后不佳。本文描述了一例健康父母的头胎女儿的病例。孕期顺利,母亲足月剖宫产。出生时,一些畸形体征明显,如皮肤松弛多余、长头畸形、前额突出、眼窝深陷、小颌畸形、肘部挛缩、蜘蛛指(趾)和髋关节发育不良。超声心动图显示二尖瓣和三尖瓣反流以及主动脉弓延长。新生儿马凡综合征的诊断得以确立,基因研究发现原纤维蛋白1(FBN1)基因存在新发突变。6个月时,由于心脏病变逐渐恶化,她接受了二尖瓣成形术。她现在2岁10个月,对于患有这种疾病的孩子来说,这是一项了不起的成就。