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Prenatal therapy in developmental disorders: drug targeting via intra-amniotic injection to treat X-linked hypohidrotic ectodermal dysplasia.

作者信息

Hermes Katharina, Schneider Pascal, Krieg Peter, Dang AnhThu, Huttner Kenneth, Schneider Holm

机构信息

German Competence Centre for Children with Ectodermal Dysplasias, Department of Pediatrics, University of Erlangen-Nürnberg, Erlangen, Germany.

Department of Biochemistry, University of Lausanne, Lausanne, Switzerland.

出版信息

J Invest Dermatol. 2014 Dec;134(12):2985-2987. doi: 10.1038/jid.2014.264. Epub 2014 Jun 20.

DOI:10.1038/jid.2014.264
PMID:24950237
Abstract
摘要

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