Mercuri Angela, Cannata Elisa, Perbellini Omar, Cugno Chiara, Balter Rita, Zaccaron Ada, Tridello Gloria, Pizzolo Giovanni, De Bortoli Massimiliano, Krampera Mauro, Cipolli Marco, Cesaro Simone
Pediatric Hematology, University of Verona, Verona, Italy.
Section of Hematology, Department of Medicine, University of Verona, Verona, Italy.
Eur J Haematol. 2015 Oct;95(4):308-15. doi: 10.1111/ejh.12490. Epub 2015 Feb 10.
Shwachman-Diamond syndrome is a rare disorder characterized by exocrine pancreatic insufficiency, skeletal abnormalities, and bone marrow failure, with high risk of leukemic evolution. The aim of the study was the immunophenotypic characterization of bone marrow cells from patients with Shwachman-Diamond syndrome to assess the maturation pathway of blood progenitor cells and to identify the presence of recurrent abnormalities.
Bone marrow samples from nineteen patients and eleven controls were analyzed by multiparameter flow cytometry.
We found a low frequency of CD34+ cells (P = 0.0179) and myeloid progenitors (P = 0.025), in the bone marrow of patients with Shwachman-Diamond syndrome as compared to the controls. A significant reduction in the percentage of granulocytes (P = 0.002) and an increase of monocytes (P < 0.001) were also evident in the bone marrow of patients.
On the basis of these observations, future prospective assessments may be useful to verify the contribution of bone marrow immunophenotype in the early identification of the evolution toward aplasia or myelodysplasia.
施瓦赫曼-戴蒙德综合征是一种罕见疾病,其特征为外分泌胰腺功能不全、骨骼异常和骨髓衰竭,白血病进展风险高。本研究的目的是对施瓦赫曼-戴蒙德综合征患者的骨髓细胞进行免疫表型分析,以评估造血祖细胞的成熟途径,并确定是否存在复发性异常。
采用多参数流式细胞术分析19例患者和11例对照的骨髓样本。
与对照组相比,我们发现施瓦赫曼-戴蒙德综合征患者骨髓中CD34+细胞(P = 0.0179)和髓系祖细胞(P = 0.025)的频率较低。患者骨髓中粒细胞百分比显著降低(P = 0.002),单核细胞增加(P < 0.001)也很明显。
基于这些观察结果,未来的前瞻性评估可能有助于验证骨髓免疫表型在早期识别向再生障碍或骨髓发育异常演变中的作用。