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Chronic ivacaftor treatment: getting F508del-CFTR into more trouble?

作者信息

Mall Marcus A, Sheppard David N

机构信息

Department of Translational Pulmonology, Translational Lung Research Center Heidelberg (TLRC), University of Heidelberg, Member of the German Center for Lung Research (DZL), Im Neuenheimer Feld 350, 69120, Heidelberg, Germany; Division of Pediatric Pulmonology & Cystic Fibrosis Center, University of Heidelberg, Member of the German Center for Lung Research (DZL), Heidelberg, Germany.

School of Physiology and Pharmacology, University of Bristol, Medical Sciences Building, University Walk, Bristol BS8 1TD, Bristol, UK.

出版信息

J Cyst Fibros. 2014 Dec;13(6):605-7. doi: 10.1016/j.jcf.2014.10.001. Epub 2014 Oct 16.

Abstract
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