Özylmaz Berk, Gezdirici Alper, Özen Mustafa, Kalenderer Önder
Departments of aMedical Genetics bOrthopedics and Traumatology, Tepecik Education and Research Hospital, Izmir cDepartment of Medical Genetics, Kanuni Sultan Suleyman Training and Research Hospital, Istanbul dDepartment of Medical Genetics, Istanbul University Cerrahpasa Medical School, Istanbul, Turkey.
Clin Dysmorphol. 2015 Apr;24(2):79-83. doi: 10.1097/MCD.0000000000000067.
Craniofrontonasal syndrome (CFNS, OMIM 304110) paradoxically presents a severe phenotype in heterozygous females and a mild or a normal phenotype in hemizygous males. Hypertelorism is seen in almost all of the female CFNS patients; craniosynostosis, facial asymmetry, and bifid nose are the other major clinical features. Most of the males are mildly affected, frequently only with hypertelorism. Here, we report a family with a G151S mutation in the EFNB1 gene. The mutation was identified in two severely affected sisters and paradoxically in their clinically unaffected father. The father on whom we report is the first male patient genetically proved to carry a CFNS-causing mutation and not presenting any signs nor symptoms of CFNS.
颅额鼻综合征(CFNS,OMIM 304110)表现出一种矛盾的现象,杂合子女性呈现严重表型,而半合子男性则表现为轻度或正常表型。几乎所有女性CFNS患者都有眼距过宽的症状;颅骨缝早闭、面部不对称和鼻裂是其他主要临床特征。大多数男性受影响较轻,通常仅表现为眼距过宽。在此,我们报告一个家族,其EFNB1基因存在G151S突变。该突变在两名严重受影响的姐妹中被发现,而矛盾的是,她们临床上未受影响的父亲也携带此突变。我们所报告的这位父亲是首个经基因检测证实携带导致CFNS突变但未出现任何CFNS体征和症状的男性患者。