Infinity Pharmaceuticals, Inc., Cambridge, MA, United States of America.
PLoS One. 2014 Dec 26;9(12):e115228. doi: 10.1371/journal.pone.0115228. eCollection 2014.
HSP90 inhibitors are currently undergoing clinical evaluation in combination with antimitotic drugs in non-small cell lung cancer (NSCLC), but little is known about the cellular effects of this novel drug combination. Therefore, we investigated the molecular mechanism of action of IPI-504 (retaspimycin HCl), a potent and selective inhibitor of HSP90, in combination with the microtubule targeting agent (MTA) docetaxel, in preclinical models of NSCLC. We identified a subset of NSCLC cell lines in which these drugs act in synergy to enhance cell death. Xenograft models of NSCLC demonstrated tumor growth inhibition, and in some cases, regression in response to combination treatment. Treatment with IPI-504 enhanced the antimitotic effects of docetaxel leading to the hypothesis that the mitotic checkpoint is required for the response to drug combination. Supporting this hypothesis, overriding the checkpoint with an Aurora kinase inhibitor diminished the cell death synergy of IPI-504 and docetaxel. To investigate the molecular basis of synergy, an unbiased stable isotope labeling by amino acids in cell culture (SILAC) proteomic approach was employed. Several mitotic regulators, including components of the ubiquitin ligase, anaphase promoting complex (APC/C), were specifically down-regulated in response to combination treatment. Loss of APC/C by RNAi sensitized cells to docetaxel and enhanced its antimitotic effects. Treatment with a PLK1 inhibitor (BI2536) also sensitized cells to IPI-504, indicating that combination effects may be broadly applicable to other classes of mitotic inhibitors. Our data provide a preclinical rationale for testing the combination of IPI-504 and docetaxel in NSCLC.
HSP90 抑制剂目前正在与非小细胞肺癌 (NSCLC) 的抗有丝分裂药物联合进行临床评估,但对于这种新型药物组合的细胞效应知之甚少。因此,我们研究了 HSP90 的强效和选择性抑制剂 IPI-504(盐酸 retaspimycin)与微管靶向药物(MTA)多西他赛联合应用于 NSCLC 临床前模型中的分子作用机制。我们鉴定了一组 NSCLC 细胞系,这些药物在这些细胞系中协同作用以增强细胞死亡。NSCLC 的异种移植模型显示肿瘤生长抑制,并且在某些情况下,对联合治疗有消退反应。用 IPI-504 处理可增强多西他赛的抗有丝分裂作用,这导致了有丝分裂检查点对于药物组合反应是必需的假设。支持这一假设,用 Aurora 激酶抑制剂覆盖检查点会减弱 IPI-504 和多西他赛的细胞死亡协同作用。为了研究协同作用的分子基础,我们采用了无偏稳定同位素标记通过氨基酸在细胞培养物(SILAC)蛋白质组学方法。几种有丝分裂调节剂,包括泛素连接酶和后期促进复合物 (APC/C) 的成分,在联合处理时特异性下调。用 RNAi 敲除 APC/C 可使细胞对多西他赛敏感并增强其抗有丝分裂作用。用 PLK1 抑制剂(BI2536)处理也可使细胞对 IPI-504 敏感,表明组合效果可能广泛适用于其他有丝分裂抑制剂。我们的数据为在 NSCLC 中测试 IPI-504 和多西他赛联合治疗提供了临床前依据。