A shot in the bone corrects a genetic disease.
作者信息
Brown Brian D
机构信息
Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, New York USA.
出版信息
Mol Ther. 2015 Apr;23(4):614-5. doi: 10.1038/mt.2015.38.
Abstract
摘要
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本文引用的文献
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Intraosseous delivery of lentiviral vectors targeting factor VIII expression in platelets corrects murine hemophilia A.
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